Announcements Trials
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Phase

Phase 1/2 1Phase 1 1

Status

Recruiting 2Unknown 1

Sponsor Class

OTHER 3

Study Type

Interventional 2Observational 1

Sponsor

Cancer Type

Myeloid 4Plasma cell 3Classical hematology 3CNS 3Endocrine 2Sarcoma 1Other solid neoplasm 1Other hematologic neoplasm 1Other 1Lymphoid 1Head & Neck 1Dermatologic 1

Conditions

Brain Neoplasms 2317Glioblastoma 2018Glioma 1403Central Nervous System Neoplasms 692Astrocytoma 668Neuroblastoma 647Gliosarcoma 480Neoplasms 406Oligodendroglioma 405Breast Neoplasms 327Medulloblastoma 307Carcinoma, Non-Small-Cell Lung 256Meningioma 229Recurrence 224Sarcoma 215Melanoma 207Neoplasm Metastasis 202Lung Neoplasms 200Ependymoma 200Neurofibromatosis 1 169Lymphoma 162Meningeal Carcinomatosis 138Osteosarcoma 135Ovarian Neoplasms 132Wilms Tumor 123Precursor Cell Lymphoblastic Leukemia-Lymphoma 123Head and Neck Neoplasms 117Lymphoma, Non-Hodgkin 116Diffuse Intrinsic Pontine Glioma 113Rhabdomyosarcoma 107

Interventions

ganglioside, GD2 1fludarabine 1Cyclophosphamide 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

3 trials
RecentStart dateEnrollment
Gaucher Disease × CNS × Clear all
NCT03721068 2026-03-27

Study of CAR T-Cells Targeting the GD2 With IL-15+iCaspase9 for Relapsed/Refractory Neuroblastoma or Relapsed/Refractory Osteosarcoma

UNC Lineberger Comprehensive Cancer Center

Phase 1 Recruiting
18 enrolled
CNSSarcoma

Gaucher Disease, Neuroblastoma, Osteosarcoma

NCT06573723 2026-01-14

Institutional Registry of Rare Diseases

Hospital Italiano de Buenos Aires

Recruiting
380 enrolled
CNSDermatologicEndocrineMyeloidPlasma cell

Immunoglobulin G4-Related Disease, Adrenal Hyperplasia, Congenital, Amyloidosis, Cardiomyopathy, Hypertrophic, Cushing Syndrome, Demyelinating Diseases, Gaucher Disease, Hepatolenticular Degeneration, von Hippel-Lindau Disease, Hirschsprung Disease, Hypertension, Pulmonary, Mastocytosis, Metabolism, Inborn Errors, Multiple Endocrine Neoplasia, Paraganglioma, Pheochromocytoma, Prader-Willi Syndrome, Sarcoidosis, Telangiectasia, Hereditary Hemorrhagic, Inflammatory Bowel Diseases, Neurocutaneous Syndromes, Rare Diseases, Vascular Malformations, Angioedemas, Hereditary, Eosinophilic Esophagitis

NCT04637503 2020-11-19

4SCAR-T Therapy Targeting GD2, PSMA and CD276 for Treating Neuroblastoma

Shenzhen Geno-Immune Medical Institute

Phase 1/2 Unknown
100 enrolled
CNS

Gaucher Disease, Neuroblastoma

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