Announcements Trials
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Phase

Phase EARLY_PHASE1 2Phase 2 2Phase 1 2

Status

Active not recruiting 3Terminated 2Completed 1

Sponsor Class

OTHER 4INDUSTRY 2

Study Type

Interventional 6

Sponsor

Cancer Type

Tumor-Agnostic 9Gynecologic 7CNS 6Thoracic 2Sarcoma 1Lymphoid 1

Conditions

Neuroblastoma 44Brain Neoplasms 18Central Nervous System Neoplasms 12Glioma 11Medulloblastoma 8Neoplasms 6Gliosarcoma 6Glioblastoma 6Ganglioneuroblastoma 6Astrocytoma 6Sarcoma, Ewing 5Sarcoma 5Rhabdomyosarcoma 5Rhabdoid Tumor 5Recurrence 5Meningeal Carcinomatosis 5Wilms Tumor 3Precursor Cell Lymphoblastic Leukemia-Lymphoma 3Oligodendroglioma 3Lymphoma 3Familial ependymoma 3Dendritic Cell Sarcoma, Interdigitating 3Burkitt Lymphoma 3Testicular Neoplasms 2Retinoblastoma 2Ovarian Neoplasms 2Osteosarcoma 2Optic Nerve Glioma 2Neuroectodermal Tumors, Primitive, Peripheral 2Neoplasm Metastasis 2

Interventions

Temozolomide 19Bevacizumab 14Irinotecan 12Carboplatin 10Cyclophosphamide 9Radiosurgery 8Lomustine 8Radiotherapy 7pembrolizumab 6Vincristine 6Topotecan 6Drug Therapy 6Surgical Procedures, Operative 5Etoposide 5Doxorubicin 5Cisplatin 53-Iodobenzylguanidine 5trametinib 4Metformin 4Gemcitabine 4Dexamethasone 4Blood Specimen Collection 4poly ICLC 3dabrafenib 3Vorinostat 3Trastuzumab 3Therapeutics 3Radiation 3Paclitaxel 3Observation 3

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

6 trials
RecentStart dateEnrollment
Neoplasms × Topotecan × CNS × Clear all
NCT05421897 2026-01-29

RAPID

Children's Hospital Los Angeles

Phase 1 Active not recruiting
11 enrolled
CNS

Neoplasms, Neuroblastoma

NCT04947501 2025-08-05

A Study of N9 Chemotherapy in Children With Neuroblastoma

Memorial Sloan Kettering Cancer Center

Phase EARLY_PHASE1 Active not recruiting
26 enrolled
CNS

Neoplasms, Neuroblastoma

NCT04239092 2025-07-17

9-ING-41 in Pediatric Patients With Refractory Malignancies.

Actuate Therapeutics Inc.

Phase 1 Terminated
40 enrolled
CNS

Diffuse Intrinsic Pontine Glioma, Meningioma, Neoplasms, Neuroblastoma

NCT03709680 2025-01-14

Study Of Palbociclib Combined With Chemotherapy In Pediatric Patients With Recurrent/Refractory Solid Tumors

Pfizer

Phase 2 Active not recruiting
128 enrolled
CNSSarcoma

Diffuse Intrinsic Pontine Glioma, Bone Neoplasms, Medulloblastoma, Neoplasms, Neuroblastoma, Rhabdomyosarcoma, Sarcoma, Sarcoma, Ewing, Rhabdoid Tumor

NCT02500459 2019-03-01

Topotecan in Glioma Undergoing A Clinically-Indicated Surgical Resection

Case Comprehensive Cancer Center

Phase EARLY_PHASE1 Terminated
9 enrolled
CNS

Brain Neoplasms, Glioma, Neoplasms

NCT00135135 2008-06-03

Therapy for Children With Neuroblastoma

St. Jude Children's Research Hospital

Phase 2 Completed
23 enrolled
CNS

Neoplasms, Neuroblastoma

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