Announcements Trials
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Phase

Phase NA 1Phase 2 1

Status

Completed 13Recruiting 7Active not recruiting 5Terminated 2Enrolling by invitation 2Withdrawn 1Unknown 1

Sponsor Class

OTHER 2INDUSTRY 2NIH 1

Study Type

Observational 3Interventional 2

Sponsor

Cancer Type

CNS 5Sarcoma 1

Conditions

Brain Neoplasms 151Glioblastoma 147Glioma 95Neuroblastoma 50Medulloblastoma 33Central Nervous System Neoplasms 27Astrocytoma 27Neoplasms 24Ependymoma 23Sarcoma 22Carcinoma, Non-Small-Cell Lung 22Neurofibromatosis 1 21Melanoma 20Breast Neoplasms 20Rhabdomyosarcoma 18Osteosarcoma 18Sarcoma, Ewing 16Lung Neoplasms 16Gliosarcoma 16Rhabdoid Tumor 15Oligodendroglioma 15Diffuse Intrinsic Pontine Glioma 14Wilms Tumor 13Meningioma 13Hepatoblastoma 13Recurrence 12Neurofibroma, Plexiform 11Neoplasm Metastasis 11Meningeal Carcinomatosis 11Lymphoma, Non-Hodgkin 11

Interventions

mirdametinib 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

5 trials
RecentStart dateEnrollment
Active not recruiting × Neurofibroma × CNS × Clear all
NCT00924196 2026-06-04

Natural History Study of Patients With Neurofibromatosis Type I

National Institutes of Health Clinical Center (CC)

Active not recruiting
259 enrolled
CNSSarcoma

Neurofibroma, Neurofibromatosis 1, Neurofibroma, Plexiform, Neurofibrosarcoma, Optic Nerve Glioma

NCT03962543 2026-05-06

ReNeu

Merck Healthcare KGaA, Darmstadt, Germany, an affiliate of Merck KGaA, Darmstadt, Germany

Phase 2 Active not recruiting
114 enrolled 25 charts 1 FDA
CNS

Neurofibroma, Neurofibromatosis 1, Neurofibromatoses, Neurofibroma, Plexiform

NCT05581511 2025-10-14

cNF Natural Hx

Johns Hopkins University

Active not recruiting
500 enrolled
CNS

Neurofibroma, Neurofibromatosis 1, Neurofibromatoses

NCT05891847 2025-06-10

Non-interventional Study of Patients With PN NF1 Starting Selumetinib in Russia

AstraZeneca

Active not recruiting
150 enrolled
CNS

Neurofibroma

NCT03820778 2021-03-02

Whole Body MRI to Identify Atypical Neurofibromas in Patients With NF1

Children's National Research Institute

Phase NA Active not recruiting
10 enrolled
CNS

Neurofibromatosis, type 4, of Riccardi, Neurofibroma, Neurofibromatosis 1, Neurofibroma, Plexiform

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