Announcements Trials
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Phase

Phase 1 1

Status

Completed 78Recruiting 26Active not recruiting 21Unknown 18Terminated 10Not yet recruiting 10Withdrawn 3Enrolling by invitation 2Suspended 1

Sponsor Class

OTHER 2

Study Type

Observational 1Interventional 1

Sponsor

Cancer Type

CNS 2

Conditions

Brain Neoplasms 12Glioblastoma 6Glioma 5Epilepsy 5Stroke 3Pheochromocytoma 3Parkinson Disease 3Paraganglioma 3Neuroblastoma 3Neoplasms 3Speech 2Neurofibromatosis 1 2Neurofibroma 2Multiple Sclerosis 2Migraine Disorders 2Lung Neoplasms 2Diabetes Mellitus 2Carcinoma, Non-Small-Cell Lung 2Amyotrophic Lateral Sclerosis 2Adrenal Gland Neoplasms 2Tinnitus 1Thyroid Neoplasms 1Tension-Type Headache 1Stress Disorders, Post-Traumatic 1Squamous Cell Carcinoma of Head and Neck 1Spinal Stenosis 1Spinal Cord Injuries 1Skin Neoplasms 1Restless Legs Syndrome 1Renal Insufficiency, Chronic 1

Interventions

Deoxycholic Acid 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

2 trials
RecentStart dateEnrollment
Enrolling by invitation × Neurofibromatosis 1 × CNS × Clear all
NCT06300502 2026-04-22

Assessing the Efficacy of Repeat, Monthly Treatments of Deoxycholate for NF1 Associated Cutaneous Neurofibromas (cNFs)

Massachusetts General Hospital

Phase 1 Enrolling by invitation
15 enrolled
CNS

Neurofibroma, Neurofibromatosis 1

NCT05238909 2025-09-02

Developing Biomarkers of Plexiform Tumor Burden in Patients With Neurofibromatosis-Type 1

Ann & Robert H Lurie Children's Hospital of Chicago

Enrolling by invitation
200 enrolled
CNS

Neurofibroma, Neurofibromatosis 1, Neurofibroma, Plexiform

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