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Phase

Phase 1 1

Status

Terminated 1

Sponsor Class

INDUSTRY 1

Study Type

Interventional 1

Sponsor

Cancer Type

Sarcoma 1CNS 1

Conditions

Glioma 8Glioblastoma 6Medulloblastoma 4Diffuse Intrinsic Pontine Glioma 4Brain Neoplasms 4Neuroblastoma 3Astrocytoma 3Rhabdoid Tumor 2Recurrence 2Neoplasms 2Meningioma 2Rhabdomyosarcoma 1Pyloric Stenosis, Hypertrophic 1Pinealoma 1Oligodendroglioma 1Neuroectodermal Tumors, Primitive 1Neoplasms, Neuroepithelial 1Neoplasms, Germ Cell and Embryonal 1Microphthalmia, Isolated, with Coloboma 5 1Lymphoma, Follicular 1Familial ependymoma 1Ependymoma 1Choroid Plexus Carcinoma 1Central Nervous System Neoplasms 1Breast Neoplasms 1

Interventions

Temozolomide 8Irinotecan 7Melphalan 6Cyclophosphamide 6X-Rays 5Topotecan 5Phantoms, Imaging 5Magnetic Resonance Spectroscopy 5Granulocyte Colony-Stimulating Factor 5Specimen Handling 4Nuclear Medicine Department, Hospital 4Busulfan 4palbociclib 3fludarabine 3Vincristine 3Thiotepa 3Stem Cell Transplantation 3Sirolimus 3Nivolumab 3Etoposide 3Bone Marrow Transplantation 3Biopsy 3ulixertinib 2tipifarnib 2thymoglobulin 2tazemetostat 2selpercatinib 2omburtamab I-131 2olaparib 2larotrectinib 2

Date Range

30 days90 days1 yearAll

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Clinical Trials

1 trials
RecentStart dateEnrollment
Rhabdomyosarcoma × ribociclib × CNS × Clear all
NCT05429502 2025-10-10

Study of Efficacy and Safety of Ribociclib (LEE011) in Combination With Topotecan and Temozolomide (TOTEM) in Pediatric Patients With Relapsed or Refractory Neuroblastoma and Other Solid Tumors

Novartis

Phase 1 Terminated
12 enrolled
CNSSarcoma

Glioma, Medulloblastoma, Neuroblastoma, Recurrence, Rhabdomyosarcoma

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