Announcements Trials
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Phase

Phase 2 1

Status

Completed 1

Sponsor Class

OTHER 1

Study Type

Interventional 1

Sponsor

Cancer Type

Classical hematology 1

Conditions

Precursor Cell Lymphoblastic Leukemia-Lymphoma 2Leukemia, Myelomonocytic, Chronic 2Leukemia, Myeloid, Acute 2Thrombocythemia, Essential 1Shwachman-Diamond Syndrome 1Primary Myelofibrosis 1Precursor T-Cell Lymphoblastic Leukemia-Lymphoma 1Polycythemia Vera 1Myelodysplastic Syndromes 1Multiple Myeloma 1Lymphoma, Non-Hodgkin 1Leukemia, Myelogenous, Chronic, BCR-ABL Positive 1Leukemia, Lymphocytic, Chronic, B-Cell 1Leukemia, Biphenotypic, Acute 1Hodgkin Disease 1Hemoglobinuria, Paroxysmal 1Congenital amegakaryocytic thrombocytopenia 1Clonal Cytopenia of Undetermined Significance 1Bone Marrow Failure Disorders 1Anemia, Refractory, with Excess of Blasts 1Anemia, Hypochromic 1Anemia, Diamond-Blackfan 1Anemia, Aplastic 1

Interventions

fludarabine phosphate 4fludarabine 3Cyclophosphamide 3Busulfan 3Antilymphocyte Serum 3Whole-Body Irradiation 2Thiotepa 2Tacrolimus 2Peripheral Blood Stem Cell Transplantation 2Melphalan 2Bone Marrow Transplantation 2Alemtuzumab 2treosulfan 1thymoglobulin 1X-Rays 1Specimen Handling 1Passive Cutaneous Anaphylaxis 1Mycophenolic Acid 1Morphine 1Methylprednisolone Hemisuccinate 1Methylprednisolone 1Methotrexate 1Methadone 1Hydromorphone 1Genetic Counseling 1Erythrocyte Transfusion 1Emapalumab 1Cyclosporins 1Clofarabine 1Clinical Trials, Phase I as Topic 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

1 trials
RecentStart dateEnrollment
Bone Marrow Failure Disorders × X-Rays × Classical hematology × Clear all
NCT04965597 2026-03-09

Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)

Fred Hutchinson Cancer Center

Phase 2 Completed
40 enrolled
Classical hematology

Congenital amegakaryocytic thrombocytopenia, Bone Marrow Failure Disorders, Shwachman-Diamond Syndrome, Anemia, Hypochromic, Hemoglobinuria, Paroxysmal, Anemia, Diamond-Blackfan

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