Announcements Trials
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Phase

Phase 1 1

Status

Recruiting 2Active not recruiting 1

Sponsor Class

OTHER 1INDUSTRY 1

Study Type

Observational 1Interventional 1

Sponsor

Cancer Type

Other hematologic neoplasm 6Myeloid 3Lymphoid 2Classical hematology 2Sarcoma 1Other solid neoplasm 1Gynecologic 1Gastrointestinal 1Endocrine 1Dermatologic 1CNS 1Breast 1

Conditions

Leukemia, Myeloid, Acute 38Anemia, Refractory, with Excess of Blasts 31Venous Thromboembolism 24Myelodysplastic Syndromes 21Neoplasms 16Precursor Cell Lymphoblastic Leukemia-Lymphoma 15Leukemia 14Anemia, Aplastic 14Thrombocytopenia 10Lymphoma, Non-Hodgkin 10Lymphoma 10Leukemia, Myelomonocytic, Chronic 10Myeloproliferative Disorders 9Anemia 9Venous Thrombosis 8Primary Myelofibrosis 8Multiple Myeloma 8Hodgkin Disease 8Hematologic Neoplasms 8Cytopenia 8Leukemia, Myelogenous, Chronic, BCR-ABL Positive 7Febrile Neutropenia 7Congenital Bone Marrow Failure Syndromes 7Anemia, Sickle Cell 7Pulmonary Embolism 6Leukemia, Lymphocytic, Chronic, B-Cell 6Leukemia, Biphenotypic, Acute 6Fanconi Anemia 6Bone Marrow Failure Disorders 6Immunologic Deficiency Syndromes 5

Interventions

venetoclax 1Azacitidine 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

2 trials
RecentStart dateEnrollment
Recruiting × GATA2 Deficiency × Classical hematology × Clear all
NCT06372717 2026-06-01

A Study to Investigate APL-4098 Alone and in Combination in Adults With AML or MDS

Apollo Therapeutics Ltd

Phase 1 Recruiting
100 enrolled
Classical hematologyOther hematologic neoplasm

GATA2 Deficiency, Anemia, Refractory, with Excess of Blasts, Leukemia, Myeloid, Acute

NCT03050268 2026-04-23

SJFAMILY

St. Jude Children's Research Hospital

Recruiting
1,500 enrolled
BreastCNSClassical hematologyDermatologicEndocrineGastrointestinalGynecologicLymphoidOther solid neoplasmSarcoma

Turcot syndrome, Juvenile polyposis syndrome, Choroid Plexus Carcinoma, GATA2 Deficiency, Basal Cell Nevus Syndrome, Colorectal Neoplasms, Hereditary Nonpolyposis, Fanconi Anemia, Hamartoma Syndrome, Multiple, von Hippel-Lindau Disease, Hodgkin Disease, Lymphoma, Non-Hodgkin, Melanoma, Neuroblastoma, Neurofibromatosis 1, Noonan Syndrome, Pancreatic Neoplasms, Paraganglioma, Peutz-Jeghers Syndrome, Pheochromocytoma, Rothmund-Thomson Syndrome, Adenomatous Polyposis Coli, Retinoblastoma, Rhabdomyosarcoma, Tuberous Sclerosis, Neurofibromatosis 2, Li-Fraumeni Syndrome, Adrenocortical Carcinoma, Multiple Endocrine Neoplasia Type 1, Multiple Endocrine Neoplasia Type 2a, Dyskeratosis Congenita, Genetic Predisposition to Disease, Anemia, Diamond-Blackfan, Carney Complex, Hereditary Breast and Ovarian Cancer Syndrome

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