Announcements Trials
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Phase

Phase 2 1

Status

Completed 1

Sponsor Class

OTHER 1

Study Type

Interventional 1

Sponsor

Cancer Type

Classical hematology 1

Conditions

Shwachman-Diamond Syndrome 1Leukemia, Myeloid, Acute 1Hemoglobinuria, Paroxysmal 1Congenital amegakaryocytic thrombocytopenia 1Bone Marrow Failure Disorders 1Anemia, Refractory, with Excess of Blasts 1Anemia, Hypochromic 1Anemia, Diamond-Blackfan 1

Interventions

fludarabine phosphate 6Whole-Body Irradiation 5Peripheral Blood Stem Cell Transplantation 5Melphalan 5Tacrolimus 3Mycophenolic Acid 3Methotrexate 3Busulfan 3thymoglobulin 2Cyclosporine 2Cyclophosphamide 2Antilymphocyte Serum 2Alemtuzumab 2treosulfan 1sargramostim 1ravulizumab 1merphos 1bryostatin 1 1X-Rays 1Transplantation, Homologous 1Sirolimus 1Observation 1Granulocyte-Macrophage Colony-Stimulating Factor 1Etoposide 1Cyclosporins 1Bryostatins 1Bone Marrow Transplantation 1Basiliximab 1

Date Range

30 days90 days1 yearAll

Options

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Clinical Trials

1 trials
RecentStart dateEnrollment
Hemoglobinuria, Paroxysmal × treosulfan × Classical hematology × Clear all
NCT04965597 2026-03-09

Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)

Fred Hutchinson Cancer Center

Phase 2 Completed
40 enrolled
Classical hematology

Congenital amegakaryocytic thrombocytopenia, Bone Marrow Failure Disorders, Shwachman-Diamond Syndrome, Anemia, Hypochromic, Hemoglobinuria, Paroxysmal, Anemia, Diamond-Blackfan

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