Announcements Trials
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Phase

Phase 3 1

Status

Completed 8Unknown 4Recruiting 4Withdrawn 2Enrolling by invitation 1Active not recruiting 1

Sponsor Class

OTHER 3INDUSTRY 1

Study Type

Observational 3Interventional 1

Sponsor

Cancer Type

Classical hematology 4Lymphoid 3Plasma cell 2Other hematologic neoplasm 2Myeloid 2Genitourinary 1CNS 1

Conditions

Leukemia, Myeloid, Acute 38Anemia, Refractory, with Excess of Blasts 31Venous Thromboembolism 24Myelodysplastic Syndromes 21Neoplasms 16Precursor Cell Lymphoblastic Leukemia-Lymphoma 15Leukemia 14Anemia, Aplastic 14Thrombocytopenia 10Lymphoma, Non-Hodgkin 10Lymphoma 10Leukemia, Myelomonocytic, Chronic 10Myeloproliferative Disorders 9Anemia 9Venous Thrombosis 8Primary Myelofibrosis 8Multiple Myeloma 8Hodgkin Disease 8Hematologic Neoplasms 8Cytopenia 8Leukemia, Myelogenous, Chronic, BCR-ABL Positive 7Febrile Neutropenia 7Congenital Bone Marrow Failure Syndromes 7Anemia, Sickle Cell 7Pulmonary Embolism 6Leukemia, Lymphocytic, Chronic, B-Cell 6Leukemia, Biphenotypic, Acute 6Fanconi Anemia 6Bone Marrow Failure Disorders 6Immunologic Deficiency Syndromes 5

Interventions

Blood Specimen Collection 1BIVV001 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

4 trials
RecentStart dateEnrollment
Recruiting × Hemophilia A × Classical hematology × Clear all
NCT06147414 2026-04-23

DANNIgene

Assistance Publique - Hôpitaux de Paris

Recruiting
550 enrolled
CNSClassical hematologyGenitourinary

Hydrocephalus, X-linked, Neurofibromatosis-Noonan syndrome, Anemia, Sickle Cell, Hemophilia B, Cystic Fibrosis, Fragile X Syndrome, Hemophilia A, Huntington Disease, Myotonic Dystrophy, Polycystic Kidney, Autosomal Recessive, Neurofibromatoses, Muscular Dystrophy, Duchenne

NCT06716814 2026-04-20

LIBERTY

Swedish Orphan Biovitrum

Phase 3 Recruiting
104 enrolled
Classical hematologyLymphoid

Blood Coagulation Disorders, Hemophilia A, Lymphoma, Follicular, Coagulation Protein Disorders

NCT04645199 2026-02-12

NICHE

Institute of Hematology & Blood Diseases Hospital, China

Recruiting
2,300 enrolled
Classical hematologyLymphoidMyeloidOther hematologic neoplasmPlasma cell

Anemia, Aplastic, Anemia, Hemolytic, Autoimmune, Hemophilia B, Hemoglobinuria, Paroxysmal, Hemophilia A, Leukemia, Lymphoma, Multiple Myeloma, Myelodysplastic Syndromes, Thrombocythemia, Essential, Leukemia, Myeloid, Acute, Hemostatic Disorders, Leukemia, Large Granular Lymphocytic

NCT07205523 2025-10-03

HALO-SCT

Affiliated Hospital of Qinghai University

Recruiting
1,000 enrolled
Classical hematologyLymphoidMyeloidOther hematologic neoplasmPlasma cell

Anemia, Aplastic, Hemophilia A, Leukemia, Lymphoma, Multiple Myeloma, Myelodysplastic Syndromes, Leukemia, Myeloid, Acute, Hemostatic Disorders

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