Announcements Trials
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Phase

Phase 2 1

Status

Recruiting 2Completed 1

Sponsor Class

OTHER 2NIH 1

Study Type

Observational 2Interventional 1

Sponsor

Cancer Type

Classical hematology 3Other hematologic neoplasm 1Dermatologic 1

Conditions

Leukemia, Myeloid, Acute 27Anemia, Refractory, with Excess of Blasts 27Myelodysplastic Syndromes 22Myeloproliferative Disorders 14Venous Thromboembolism 13Precursor Cell Lymphoblastic Leukemia-Lymphoma 13Neoplasms 11Lymphoma, Non-Hodgkin 11Leukemia, Myelomonocytic, Chronic 10Anemia 10Primary Myelofibrosis 9Hematologic Neoplasms 9Anemia, Aplastic 9Leukemia, Lymphocytic, Chronic, B-Cell 8Hodgkin Disease 8Thrombocytopenia 7Leukemia, Myelogenous, Chronic, BCR-ABL Positive 7Leukemia 7Fanconi Anemia 7Multiple Myeloma 6Congenital Bone Marrow Failure Syndromes 6Venous Thrombosis 5Pulmonary Embolism 5Myelodysplastic-Myeloproliferative Diseases 5Lymphoma, Follicular 5Febrile Neutropenia 5Anemia, Sickle Cell 5Recurrence 4Leukemia, Myeloid, Accelerated Phase 4Leukemia, Biphenotypic, Acute 4

Interventions

treosulfan 1thymoglobulin 1fludarabine phosphate 1X-Rays 1Tacrolimus 1Peripheral Blood Stem Cell Transplantation 1Methotrexate 1Bone Marrow Transplantation 1Antilymphocyte Serum 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

3 trials
RecentStart dateEnrollment
Shwachman-Diamond Syndrome × Classical hematology × 90 days × Clear all
NCT00027274 2026-06-02

Cancer in Inherited Bone Marrow Failure Syndromes

National Institutes of Health Clinical Center (CC)

Recruiting
4,000 enrolled
Classical hematologyDermatologic

Congenital Bone Marrow Failure Syndromes, Shwachman-Diamond Syndrome, Anemia, Aplastic, Fanconi Anemia, Dyskeratosis Congenita, Anemia, Diamond-Blackfan

NCT06056908 2026-04-06

SDSR

Boston Children's Hospital

Recruiting
5,000 enrolled
Classical hematologyOther hematologic neoplasm

Bone Marrow Failure Disorders, Congenital Bone Marrow Failure Syndromes, Shwachman-Diamond Syndrome, Leukemia, Neutropenia

NCT04965597 2026-03-09

Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)

Fred Hutchinson Cancer Center

Phase 2 Completed
40 enrolled
Classical hematology

Congenital amegakaryocytic thrombocytopenia, Bone Marrow Failure Disorders, Shwachman-Diamond Syndrome, Anemia, Hypochromic, Hemoglobinuria, Paroxysmal, Anemia, Diamond-Blackfan

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