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Phase

Phase 2 1

Status

Recruiting 3Completed 1

Sponsor Class

OTHER 1

Study Type

Interventional 1

Sponsor

Cancer Type

Thoracic 11Gastrointestinal 6Genitourinary 5Sarcoma 4CNS 4Breast 4Lymphoid 3Head & Neck 3Other hematologic neoplasm 2Myeloid 2Endocrine 2Dermatologic 2Plasma cell 1Other neoplasm 1Gynecologic 1Classical hematology 1

Conditions

Shwachman-Diamond Syndrome 1Hemoglobinuria, Paroxysmal 1Congenital amegakaryocytic thrombocytopenia 1Bone Marrow Failure Disorders 1Anemia, Hypochromic 1Anemia, Diamond-Blackfan 1

Interventions

fludarabine phosphate 58Cyclophosphamide 54Epoetin Alfa 43Cyclosporine 42Busulfan 42Peripheral Blood Stem Cell Transplantation 38Mycophenolic Acid 33Darbepoetin alfa 33Antilymphocyte Serum 31Cytarabine 30Whole-Body Irradiation 29Filgrastim 29Methotrexate 26Tacrolimus 25Radiotherapy 25Melphalan 24fludarabine 21Methylprednisolone 17Cord Blood Stem Cell Transplantation 17Granulocyte Colony-Stimulating Factor 13Etoposide 13Daunorubicin 13Rivaroxaban 12apixaban 11Thiotepa 11sargramostim 10epoetin beta 10Dalteparin 10eltrombopag 9Alemtuzumab 9

Date Range

30 days90 days1 yearAll

Options

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Clinical Trials

1 trials
RecentStart dateEnrollment
Completed × X-Rays × Classical hematology × Clear all
NCT04965597 2026-03-09

Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)

Fred Hutchinson Cancer Center

Phase 2 Completed
40 enrolled
Classical hematology

Congenital amegakaryocytic thrombocytopenia, Bone Marrow Failure Disorders, Shwachman-Diamond Syndrome, Anemia, Hypochromic, Hemoglobinuria, Paroxysmal, Anemia, Diamond-Blackfan

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