Announcements Trials
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Phase

Phase 2 1

Status

Not yet recruiting 1Completed 1

Sponsor Class

OTHER 1

Study Type

Interventional 1

Sponsor

Cancer Type

Other hematologic neoplasm 11Myeloid 9Lymphoid 2Sarcoma 1Gynecologic 1Genitourinary 1Classical hematology 1

Conditions

Shwachman-Diamond Syndrome 1Hemoglobinuria, Paroxysmal 1Congenital amegakaryocytic thrombocytopenia 1Bone Marrow Failure Disorders 1Anemia, Hypochromic 1Anemia, Diamond-Blackfan 1

Interventions

fludarabine phosphate 58Cyclophosphamide 54Epoetin Alfa 43Cyclosporine 43Busulfan 43Peripheral Blood Stem Cell Transplantation 39Mycophenolic Acid 34Darbepoetin alfa 33Antilymphocyte Serum 31Whole-Body Irradiation 30Cytarabine 30Filgrastim 29Methotrexate 26Tacrolimus 25Radiotherapy 25Melphalan 24fludarabine 21Methylprednisolone 17Cord Blood Stem Cell Transplantation 17Etoposide 14Granulocyte Colony-Stimulating Factor 13Daunorubicin 13Rivaroxaban 12apixaban 11Thiotepa 11sargramostim 10epoetin beta 10Dalteparin 10eltrombopag 9Alemtuzumab 9

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

1 trials
RecentStart dateEnrollment
Completed × treosulfan × Classical hematology × Clear all
NCT04965597 2026-03-09

Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)

Fred Hutchinson Cancer Center

Phase 2 Completed
40 enrolled
Classical hematology

Congenital amegakaryocytic thrombocytopenia, Bone Marrow Failure Disorders, Shwachman-Diamond Syndrome, Anemia, Hypochromic, Hemoglobinuria, Paroxysmal, Anemia, Diamond-Blackfan

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