Announcements Trials
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Phase

Phase 2 2

Status

Completed 26Unknown 8Recruiting 8Terminated 4Active not recruiting 3Withdrawn 1No longer available 1Available 1

Sponsor Class

INDUSTRY 2OTHER 1

Study Type

Interventional 2Observational 1

Sponsor

Cancer Type

Myeloid 3

Conditions

Myelodysplastic Syndromes 101Leukemia, Myeloid, Acute 80Precursor Cell Lymphoblastic Leukemia-Lymphoma 40Myeloproliferative Disorders 40Leukemia, Myelogenous, Chronic, BCR-ABL Positive 38Leukemia, Myelomonocytic, Chronic 33Primary Myelofibrosis 30Lymphoma, Non-Hodgkin 30Polycythemia Vera 19Lymphoma 15Leukemia 15Hematologic Neoplasms 15Leukemia, Biphenotypic, Acute 14Thrombocythemia, Essential 13Multiple Myeloma 11Hodgkin Disease 11Histiocytosis, Langerhans-Cell 11Neoplasms 10Leukemia, Myeloid, Chronic-Phase 10Leukemia, Lymphocytic, Chronic, B-Cell 10Rhabdoid Tumor 9Neuroblastoma 9Medulloblastoma 9Glioma 9Ependymoma 9Anemia, Refractory, with Excess of Blasts 9Wilms Tumor 8Sarcoma 8Rhabdomyosarcoma 8Osteosarcoma 8

Interventions

avapritinib 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

3 trials
RecentStart dateEnrollment
Active not recruiting × Mastocytosis, Systemic × Myeloid × Clear all
NCT05186753 2026-05-22

(Summit) A Study to Evaluate the Efficacy and Safety of CGT9486 Versus Placebo in Patients With Indolent or Smoldering Systemic Mastocytosis

Cogent Biosciences, Inc.

Phase 2 Active not recruiting
237 enrolled
Myeloid

Hematologic Diseases, Hypersensitivity, Immune Complex Diseases, Immune System Diseases, Mastocytosis, Mastocytosis, Systemic

NCT03731260 2025-09-23

(PIONEER) Study to Evaluate Efficacy and Safety of Avapritinib (BLU-285), A Selective KIT Mutation-targeted Tyrosine Kinase Inhibitor, Versus Placebo in Patients With Indolent Systemic Mastocytosis

Blueprint Medicines Corporation

Phase 2 Active not recruiting
251 enrolled
Myeloid

Mastocytosis, Systemic

NCT06065007 2025-04-04

Quality of Life and Disease-related Symptoms in Individuals With Systemic Mastocytosis

Uppsala University

Active not recruiting
400 enrolled
Myeloid

Mastocytosis, Systemic

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