Announcements Trials
Browse Landscape

Phase

Phase 2 2Phase 4 1Phase 1 1

Status

Recruiting 3Completed 1Active not recruiting 1

Sponsor Class

INDUSTRY 4OTHER 1

Study Type

Interventional 4Observational 1

Sponsor

Cancer Type

Myeloid 5Other hematologic neoplasm 3Sarcoma 2Gastrointestinal 2Tumor-Agnostic 1Thoracic 1Lymphoid 1Dermatologic 1CNS 1

Conditions

Mastocytosis, Systemic 4Systemic Mastocytosis With an Associated Hematologic Neoplasm 1Mastocytosis 1Leukemia, Mast-Cell 1

Interventions

fludarabine 63Cyclophosphamide 63venetoclax 57Azacitidine 52fludarabine phosphate 50Specimen Handling 44Whole-Body Irradiation 40ruxolitinib 37Mycophenolic Acid 37Tacrolimus 35Melphalan 32Busulfan 32Biopsy 32Cytarabine 31Stem Cell Transplantation 27Decitabine 27Granulocyte Colony-Stimulating Factor 21asciminib 19decitabine and cedazuridine drug combination 18Sirolimus 18Peripheral Blood Stem Cell Transplantation 18Injections 18Thiotepa 17Filgrastim 17nilotinib 15X-Rays 14Methotrexate 14Cyclosporine 14Imatinib Mesylate 13Magnetic Resonance Spectroscopy 12

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

5 trials
RecentStart dateEnrollment
avapritinib × Myeloid × 1 year × Clear all
NCT03580655 2026-04-24

(PATHFINDER) Study to Evaluate Efficacy and Safety of Avapritinib (BLU-285), A Selective KIT Mutation-targeted Tyrosine Kinase Inhibitor, in Patients With Advanced Systemic Mastocytosis

Blueprint Medicines Corporation

Phase 2 Completed
107 enrolled 30 charts 1 FDA
LymphoidMyeloidOther hematologic neoplasm

Leukemia, Mast-Cell, Mastocytosis, Systemic

NCT07255638 2026-04-20

A Non-Interventional Study in Participants With Indolent Systemic Mastocytosis (ISM) in Germany

Blueprint Medicines Corporation

Recruiting
80 enrolled
Myeloid

Mastocytosis, Mastocytosis, Systemic

NCT06327685 2026-04-01

Avapritinib With Decitabine in Patients With SM-AHN

H. Lee Moffitt Cancer Center and Research Institute

Phase 1 Recruiting
34 enrolled
MyeloidOther hematologic neoplasm

Systemic Mastocytosis With an Associated Hematologic Neoplasm

NCT06748001 2026-02-09

Avapritinib Rollover Study

Blueprint Medicines Corporation

Phase 4 Recruiting
60 enrolled
Myeloid

Mastocytosis, Systemic

NCT03731260 2025-09-23

(PIONEER) Study to Evaluate Efficacy and Safety of Avapritinib (BLU-285), A Selective KIT Mutation-targeted Tyrosine Kinase Inhibitor, Versus Placebo in Patients With Indolent Systemic Mastocytosis

Blueprint Medicines Corporation

Phase 2 Active not recruiting
251 enrolled
Myeloid

Mastocytosis, Systemic

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