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Status

No longer available 1Available 1

Sponsor Class

OTHER 1INDUSTRY 1

Study Type

Interventional 45Observational 18Expanded_access 2

Sponsor

Cancer Type

Sarcoma 2

Conditions

Sarcoma 13Gastrointestinal Stromal Tumors 7Ovarian Neoplasms 5Neoplasms 5Osteosarcoma 4Sarcoma, Ewing 3Prostatic Neoplasms 3Pancreatic Neoplasms 3Lymphoma 3Uterine Neoplasms 2Stomach Neoplasms 2Sarcoma, Synovial 2Rhabdoid Tumor 2Neuroectodermal Tumors, Primitive 2Multiple Myeloma 2Lymphoma, Non-Hodgkin 2Lymphoma, Large B-Cell, Diffuse 2Leukemia 2Hodgkin Disease 2Endometrial Neoplasms 2Desmoid Tumors 2Chondrosarcoma 2Carcinoma, Squamous Cell 2Carcinoma, Non-Small-Cell Lung 2Breast Neoplasms 2Wilms Tumor 1Waldenstrom Macroglobulinemia 1Uterine Cervical Neoplasms 1Rhabdomyosarcoma 1Retinoblastoma 1

Interventions

nirogacestat 2

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

2 trials
RecentStart dateEnrollment
Expanded_access × Desmoid Tumors × Sarcoma × Clear all
NCT05041036 2026-05-08

Individual Patient Compassionate Use of Nirogacestat

Merck Healthcare KGaA, Darmstadt, Germany, an affiliate of Merck KGaA, Darmstadt, Germany

Available
Sarcoma

Desmoid Tumors

NCT02955446 2019-02-01

Compassionate Use Protocol for PF-03084014 in Patients With Advanced Solid Tumor Malignancies

University of Colorado, Denver

No longer available
Sarcoma

Neoplasms, Desmoid Tumors

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