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Phase

Phase 2 1Phase 1/2 1

Status

Completed 1

Sponsor Class

OTHER 1

Study Type

Interventional 1

Sponsor

Cancer Type

Classical hematology 1

Conditions

Leukemia, Myeloid, Acute 78Myelodysplastic Syndromes 75Precursor Cell Lymphoblastic Leukemia-Lymphoma 70Leukemia, Lymphocytic, Chronic, B-Cell 58Leukemia 55Hodgkin Disease 55Lymphoma, Non-Hodgkin 54Lymphoma 48Multiple Myeloma 45Myeloproliferative Disorders 41Lymphoma, Follicular 40Graft vs Host Disease 38Lymphoma, Mantle-Cell 36Lymphoma, Large B-Cell, Diffuse 36Leukemia, Myelomonocytic, Chronic 36Lymphoma, B-Cell, Marginal Zone 35Leukemia, Myeloid, Accelerated Phase 34Leukemia, Myelogenous, Chronic, BCR-ABL Positive 33Congenital Abnormalities 33Burkitt Lymphoma 33Leukemia, Myeloid, Chronic-Phase 29Primary Myelofibrosis 28Hematologic Neoplasms 28Neoplasms, Plasma Cell 24Lymphoma, Large-Cell, Immunoblastic 24Blast Crisis 24Waldenstrom Macroglobulinemia 20Leukemia, Myeloid, Chronic, Atypical, BCR-ABL Negative 19Myelodysplastic-Myeloproliferative Diseases 18Precursor T-Cell Lymphoblastic Leukemia-Lymphoma 17

Interventions

fludarabine phosphate 5fludarabine 3Busulfan 3Antilymphocyte Serum 3Whole-Body Irradiation 2Mycophenolic Acid 2Cyclophosphamide 2Clofarabine 2Alemtuzumab 2treosulfan 1thymoglobulin 1eltrombopag 1X-Rays 1Thiotepa 1Therapeutics 1Tacrolimus 1Sirolimus 1Peripheral Blood Stem Cell Transplantation 1Methotrexate 1Melphalan 1Emapalumab 1Cyclosporins 1Bone Marrow Transplantation 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

1 trials
RecentStart dateEnrollment
Phase 2 × Bone Marrow Failure Disorders × Tacrolimus × Clear all
NCT04965597 2026-03-09

Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)

Fred Hutchinson Cancer Center

Phase 2 Completed
40 enrolled
Classical hematology

Congenital amegakaryocytic thrombocytopenia, Bone Marrow Failure Disorders, Shwachman-Diamond Syndrome, Anemia, Hypochromic, Hemoglobinuria, Paroxysmal, Anemia, Diamond-Blackfan

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