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Phase

Phase 2 1

Status

Completed 1

Sponsor Class

OTHER 1

Study Type

Interventional 1

Sponsor

Cancer Type

Classical hematology 1

Conditions

Prostatic Neoplasms 12Lymphoma, Non-Hodgkin 8Wilms Tumor 7Sarcoma 7Glioma 7Rhabdoid Tumor 6Neuroectodermal Tumors, Primitive, Peripheral 6Neuroblastoma 6Multiple Myeloma 6Medulloblastoma 6Lymphoma 6Histiocytosis, Langerhans-Cell 6Hepatoblastoma 6Ependymoma 6Rhabdomyosarcoma 5Osteosarcoma 5Central Nervous System Neoplasms 5Pancreatic Neoplasms 4Mouth Neoplasms 4Leukemia, Myeloid, Acute 4Colorectal Neoplasms 4Breast Neoplasms 4Sarcoma, Ewing 3Precursor Cell Lymphoblastic Leukemia-Lymphoma 3Myelodysplastic Syndromes 3Laryngeal Neoplasms 3Hypopharyngeal Neoplasms 3Urinary Bladder Neoplasms 2Thyroid Neoplasms 2Thyroid Cancer, Papillary 2

Interventions

fludarabine phosphate 5fludarabine 3Busulfan 3Antilymphocyte Serum 3Whole-Body Irradiation 2Mycophenolic Acid 2Cyclophosphamide 2Clofarabine 2Alemtuzumab 2treosulfan 1thymoglobulin 1eltrombopag 1X-Rays 1Thiotepa 1Therapeutics 1Tacrolimus 1Sirolimus 1Peripheral Blood Stem Cell Transplantation 1Methotrexate 1Melphalan 1Emapalumab 1Cyclosporins 1Bone Marrow Transplantation 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

1 trials
RecentStart dateEnrollment
Phase 2 × Bone Marrow Failure Disorders × X-Rays × Clear all
NCT04965597 2026-03-09

Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)

Fred Hutchinson Cancer Center

Phase 2 Completed
40 enrolled
Classical hematology

Congenital amegakaryocytic thrombocytopenia, Bone Marrow Failure Disorders, Shwachman-Diamond Syndrome, Anemia, Hypochromic, Hemoglobinuria, Paroxysmal, Anemia, Diamond-Blackfan

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