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Phase

Phase 2 1

Status

Completed 1

Sponsor Class

OTHER 1

Study Type

Interventional 1

Sponsor

Cancer Type

Classical hematology 1

Conditions

Lung Neoplasms 8Carcinoma, Non-Small-Cell Lung 6Breast Neoplasms 4Prostatic Neoplasms 3Small Cell Lung Carcinoma 2Sarcoma, Ewing 2Rectal Neoplasms 2Pulmonary Disease, Chronic Obstructive 2Melanoma 2Lymphoma, Non-Hodgkin 2Head and Neck Neoplasms 2Wilms Tumor 1Waldenstrom Macroglobulinemia 1Uterine Cervical Neoplasms 1Uterine Cervical Dysplasia 1Tuberculosis 1Thoracic Cancer 1Shwachman-Diamond Syndrome 1Sarcoma 1Rhabdomyosarcoma 1Rhabdoid Tumor 1Recurrence 1Precancerous Conditions 1Pneumonia 1Pathologic Complete Response 1Pancreatic Intraductal Neoplasms 1Osteosarcoma 1Osteoporosis 1Neurofibrosarcoma 1Neurofibromatosis 1 1

Interventions

fludarabine phosphate 3Antilymphocyte Serum 3Whole-Body Irradiation 2Cyclophosphamide 2treosulfan 1thymoglobulin 1posaconazole 1fludarabine 1X-Rays 1Thiotepa 1Tacrolimus 1Sirolimus 1Peripheral Blood Stem Cell Transplantation 1Mycophenolic Acid 1Methotrexate 1Melphalan 1Busulfan 1Bone Marrow Transplantation 1Alemtuzumab 1

Date Range

30 days90 days1 yearAll

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Clinical Trials

1 trials
RecentStart dateEnrollment
Completed × Bone Marrow Failure Disorders × X-Rays × Clear all
NCT04965597 2026-03-09

Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)

Fred Hutchinson Cancer Center

Phase 2 Completed
40 enrolled
Classical hematology

Congenital amegakaryocytic thrombocytopenia, Bone Marrow Failure Disorders, Shwachman-Diamond Syndrome, Anemia, Hypochromic, Hemoglobinuria, Paroxysmal, Anemia, Diamond-Blackfan

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