Announcements Trials
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Status

Recruiting 9Active not recruiting 4Withdrawn 1Completed 1Available 1

Sponsor Class

INDUSTRY 1

Study Type

Expanded_access 1

Sponsor

Cancer Type

Sarcoma 1

Conditions

Carcinoma, Non-Small-Cell Lung 5Pancreatic Neoplasms 3Melanoma 3Urinary Bladder Neoplasms 2Sarcoma 2Ovarian Neoplasms 2Non-Muscle Invasive Bladder Neoplasms 2Neoplasms 2Head and Neck Neoplasms 2Colorectal Neoplasms 2Carcinoma, Hepatocellular 2Breast Neoplasms 2Urologic Neoplasms 1Triple Negative Breast Neoplasms 1Thyroid Neoplasms 1Stomach Neoplasms 1Small Cell Lung Carcinoma 1Prostatic Neoplasms 1Precursor Cell Lymphoblastic Leukemia-Lymphoma 1Pancreatic Ductal Adenocarcinoma (PDAC) 1Osteosarcoma 1Neurofibromatoses 1Neurofibroma, Plexiform 1Neuroblastoma 1Myelodysplastic Syndromes 1Meningioma 1Mastocytosis, Systemic 1Lymphoma, Mantle-Cell 1Lymphoma 1Leukemia, Myeloid, Acute 1

Interventions

nirogacestat 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

1 trials
RecentStart dateEnrollment
Available × Desmoid Tumors × 90 days × Clear all
NCT05041036 2026-05-08

Individual Patient Compassionate Use of Nirogacestat

Merck Healthcare KGaA, Darmstadt, Germany, an affiliate of Merck KGaA, Darmstadt, Germany

Available
Sarcoma

Desmoid Tumors

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