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Phase

Phase 2 1Phase 1/2 1

Status

Active not recruiting 1

Sponsor Class

NETWORK 1

Study Type

Interventional 1

Sponsor

Cancer Type

Sarcoma 1

Conditions

Wilms Tumor 7Rhabdoid Tumor 6Neuroectodermal Tumors, Primitive, Peripheral 6Neuroblastoma 6Medulloblastoma 6Lymphoma, Non-Hodgkin 6Histiocytosis, Langerhans-Cell 6Hepatoblastoma 6Glioma 6Ependymoma 6Sarcoma 5Rhabdomyosarcoma 5Osteosarcoma 5Central Nervous System Neoplasms 5Sarcoma, Ewing 3Pancreatic Neoplasms 2Xanthogranuloma, Juvenile 1Thyroid Cancer, Papillary 1Precursor T-Cell Lymphoblastic Leukemia-Lymphoma 1Precursor Cell Lymphoblastic Leukemia-Lymphoma 1Neuroendocrine Tumors 1Nasopharyngeal Carcinoma 1Lymphoma, B-Cell 1Lymphoma 1Immunoglobulin Light-chain Amyloidosis 1Histiocytic Sarcoma 1Hematopoietic and Lymphatic System Neoplasm 1Familial ependymoma 1Duodenal Neoplasms 1Desmoid Tumors 1

Interventions

nirogacestat 4Toremifene 2Specimen Handling 2Magnetic Resonance Spectroscopy 2X-Rays 1Vinblastine 1Taxes 1Tamoxifen 1Sunitinib 1Sulindac 1Radiotherapy 1Phantoms, Imaging 1Nivolumab 1Methotrexate 1Ipilimumab 1Imatinib Mesylate 1Hydroxyurea 1Cryosurgery 1CTLA-4 Antigen 1Albumin-Bound Paclitaxel 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

1 trials
RecentStart dateEnrollment
Phase 2 × Desmoid Tumors × Phantoms, Imaging × Clear all
NCT04195399 2026-04-15

A Study of a New Drug, Nirogacestat, for Treating Desmoid Tumors That Cannot be Removed by Surgery

Children's Oncology Group

Phase 2 Active not recruiting
31 enrolled
Sarcoma

Desmoid Tumors

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