Announcements Trials
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Phase

Phase 2 2Phase 1/2 1

Status

Completed 2Withdrawn 1

Sponsor Class

OTHER 2NIH 1

Study Type

Interventional 3

Sponsor

Conditions

Precursor Cell Lymphoblastic Leukemia-Lymphoma 39Leukemia, Myeloid, Acute 35Myelodysplastic Syndromes 33Multiple Myeloma 30Lymphoma, Non-Hodgkin 29Hodgkin Disease 28Graft vs Host Disease 26Leukemia, Lymphocytic, Chronic, B-Cell 25Lymphoma 24Leukemia 24Hematologic Neoplasms 20Neoplasms 18Lymphoma, Mantle-Cell 18Sarcoma 17Leukemia, Myelogenous, Chronic, BCR-ABL Positive 17Breast Neoplasms 17Tuberous Sclerosis 15Myeloproliferative Disorders 15Lymphoma, Large B-Cell, Diffuse 15Lymphoma, Follicular 14Burkitt Lymphoma 14Waldenstrom Macroglobulinemia 13Lymphoma, B-Cell, Marginal Zone 13Recurrence 12Neoplasm Metastasis 12Carcinoma, Non-Small-Cell Lung 12Prostatic Neoplasms 11Primary Myelofibrosis 11Melanoma 11Leukemia, Myelomonocytic, Chronic 11

Interventions

Sirolimus 3Everolimus 2dactolisib 1Physical Examination 1Mastectomy, Subcutaneous 1Mastectomy 1Fluorodeoxyglucose F18 1Colonoscopy 18-(6-methoxypyridin-3-yl)-3-methyl-1-(4-piperazin-1-yl-3-trifluoromethylphenyl)-1,3-dihydroimidazo(4,5-c)quinolin-2-one 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

3 trials
RecentStart dateEnrollment
Hamartoma Syndrome, Multiple × Sirolimus × Clear all
NCT04094675 2025-06-10

Sirolimus for Cowden Syndrome With Colon Polyposis

Ohio State University

Phase 2 Completed
5 enrolled

Hamartoma Syndrome, Multiple

NCT06080165 2024-07-10

Sirolimus for Improving Social Abilities in People With PTEN Germline Mutations

Stanford University

Phase 1/2 Withdrawn

Hamartoma Syndrome, Multiple

NCT00971789 2015-09-30

Sirolimus to Treat Cowden Syndrome and Other PTEN Hamartomatous Tumor Syndromes

National Institutes of Health Clinical Center (CC)

Phase 2 Completed
18 enrolled 7 charts

Hamartoma Syndrome, Multiple

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