Announcements Trials
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Phase

Phase 2 1

Status

Completed 1

Sponsor Class

OTHER 1

Study Type

Interventional 1

Sponsor

Cancer Type

Classical hematology 1

Conditions

Leukemia, Myeloid, Acute 7Myelodysplastic Syndromes 6Precursor Cell Lymphoblastic Leukemia-Lymphoma 5Hematologic Neoplasms 5Lymphoma, Non-Hodgkin 4Leukemia, Myelomonocytic, Juvenile 3Leukemia, Myelogenous, Chronic, BCR-ABL Positive 3beta-Thalassemia 2Lymphoma 2Hodgkin Disease 2Anemia, Refractory, with Excess of Blasts 2Vasculitis, Central Nervous System 1Thalassemia 1Stiff-Person Syndrome 1Shwachman-Diamond Syndrome 1Sarcoma, Myeloid 1Rhabdomyosarcoma 1Rasmussen subacute encephalitis 1Primary Myelofibrosis 1Precursor T-Cell Lymphoblastic Leukemia-Lymphoma 1Polyradiculoneuropathy, Chronic Inflammatory Demyelinating 1Opsoclonus-Myoclonus Syndrome 1Non-Malignant Neoplasm 1Neuromyelitis Optica 1Neurofibrosarcoma 1Neurofibromatosis 1 1Neuroectodermal Tumors, Primitive, Peripheral 1Neuroblastoma 1Neoplasms, Plasma Cell 1Neoplasm, Residual 1

Interventions

fludarabine phosphate 3Peripheral Blood Stem Cell Transplantation 3Whole-Body Irradiation 2Tacrolimus 2Methotrexate 2Cyclophosphamide 2treosulfan 1thymoglobulin 1ravulizumab 1X-Rays 1Sirolimus 1Observation 1Mycophenolic Acid 1Melphalan 1Etoposide 1Cyclosporine 1Busulfan 1Bone Marrow Transplantation 1Antilymphocyte Serum 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

1 trials
RecentStart dateEnrollment
Hemoglobinuria, Paroxysmal × thymoglobulin × 1 year × Clear all
NCT04965597 2026-03-09

Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)

Fred Hutchinson Cancer Center

Phase 2 Completed
40 enrolled
Classical hematology

Congenital amegakaryocytic thrombocytopenia, Bone Marrow Failure Disorders, Shwachman-Diamond Syndrome, Anemia, Hypochromic, Hemoglobinuria, Paroxysmal, Anemia, Diamond-Blackfan

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