Announcements Trials
Browse Landscape

Phase

Phase 2 1

Status

Completed 1

Sponsor Class

OTHER 1

Study Type

Interventional 1

Sponsor

Cancer Type

Classical hematology 1

Conditions

Leukemia, Myeloid, Acute 3Precursor Cell Lymphoblastic Leukemia-Lymphoma 2Myelodysplastic Syndromes 2Anemia, Refractory, with Excess of Blasts 2Shwachman-Diamond Syndrome 1Recurrence 1Myelodysplastic-Myeloproliferative Diseases 1Lymphoma, Non-Hodgkin 1Leukemia, Myelomonocytic, Chronic 1Leukemia, Myeloid, Chronic-Phase 1Leukemia, Myeloid, Accelerated Phase 1Leukemia, Biphenotypic, Acute 1Hodgkin Disease 1Hemoglobinuria, Paroxysmal 1Hematologic Neoplasms 1Congenital amegakaryocytic thrombocytopenia 1Bone Marrow Failure Disorders 1Anemia, Hypochromic 1Anemia, Diamond-Blackfan 1

Interventions

fludarabine phosphate 2Tacrolimus 2Peripheral Blood Stem Cell Transplantation 2Methotrexate 2treosulfan 1thymoglobulin 1ravulizumab 1X-Rays 1Whole-Body Irradiation 1Sirolimus 1Mycophenolic Acid 1Melphalan 1Etoposide 1Cyclosporine 1Cyclophosphamide 1Busulfan 1Bone Marrow Transplantation 1Antilymphocyte Serum 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

1 trials
RecentStart dateEnrollment
Hemoglobinuria, Paroxysmal × Antilymphocyte Serum × 90 days × Clear all
NCT04965597 2026-03-09

Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)

Fred Hutchinson Cancer Center

Phase 2 Completed
40 enrolled
Classical hematology

Congenital amegakaryocytic thrombocytopenia, Bone Marrow Failure Disorders, Shwachman-Diamond Syndrome, Anemia, Hypochromic, Hemoglobinuria, Paroxysmal, Anemia, Diamond-Blackfan

Data powered by HemOnc (CC BY 4.0) Colophon âš¡