Announcements Trials
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Phase

Phase 2 1

Status

Completed 1

Sponsor Class

OTHER 1

Study Type

Interventional 1

Sponsor

Cancer Type

Classical hematology 1

Conditions

Leukemia, Myeloid, Acute 11Myelodysplastic Syndromes 10Leukemia, Myelomonocytic, Chronic 3Precursor Cell Lymphoblastic Leukemia-Lymphoma 2Leukemia, Myelogenous, Chronic, BCR-ABL Positive 2Leukemia, Biphenotypic, Acute 2Hodgkin Disease 2Uveal Melanoma 1Shwachman-Diamond Syndrome 1Prostatic Neoplasms 1Neoplasm, Residual 1Myeloproliferative Disorders 1Myelodysplastic-Myeloproliferative Diseases 1Multiple Myeloma 1Lymphoma, Non-Hodgkin 1Lymphoma, Mantle-Cell 1Lymphoma, Large-Cell, Anaplastic 1Lymphoma, Large B-Cell, Diffuse 1Lymphoma, Follicular 1Lymphoma, B-Cell, Marginal Zone 1Leukemia, Prolymphocytic 1Leukemia, Myeloid, Chronic-Phase 1Leukemia, Myeloid, Accelerated Phase 1Leukemia, Lymphocytic, Chronic, B-Cell 1Leukemia 1Hemoglobinuria, Paroxysmal 1Hematologic Neoplasms 1Graft vs Host Disease 1Congenital amegakaryocytic thrombocytopenia 1Congenital Abnormalities 1

Interventions

fludarabine phosphate 6Peripheral Blood Stem Cell Transplantation 5Melphalan 5Whole-Body Irradiation 4Mycophenolic Acid 4Tacrolimus 3Stem Cell Transplantation 3Methotrexate 3Cyclophosphamide 3Busulfan 3Alemtuzumab 3thymoglobulin 2Cyclosporine 2Antilymphocyte Serum 2Antibodies 2treosulfan 1merphos 1fludarabine 1X-Rays 1Thiotepa 1Sirolimus 1Rituximab 1Muromonab-CD3 1Granulocyte Colony-Stimulating Factor 1Filgrastim 1Etoposide 1Cyclosporins 1Bone Marrow Transplantation 1Basiliximab 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

1 trials
RecentStart dateEnrollment
Phase 2 × Hemoglobinuria, Paroxysmal × treosulfan × Clear all
NCT04965597 2026-03-09

Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)

Fred Hutchinson Cancer Center

Phase 2 Completed
40 enrolled
Classical hematology

Congenital amegakaryocytic thrombocytopenia, Bone Marrow Failure Disorders, Shwachman-Diamond Syndrome, Anemia, Hypochromic, Hemoglobinuria, Paroxysmal, Anemia, Diamond-Blackfan

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