Announcements Trials
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Phase

Phase 2 1Phase 1 1

Status

Completed 2

Sponsor Class

INDUSTRY 2

Study Type

Interventional 2

Sponsor

Cancer Type

Other hematologic neoplasm 2Myeloid 2Lymphoid 2

Conditions

Gastrointestinal Stromal Tumors 7Mastocytosis, Systemic 5Leukemia, Myeloid, Acute 5Recurrence 4Sarcoma 2Neoplasm Metastasis 2Leukemia, Mast-Cell 2Glioma 2Systemic Mastocytosis With an Associated Hematologic Neoplasm 1Neoplasms 1Neoplasm, Residual 1Melanoma 1Mastocytosis 1Lung Neoplasms 1Glioblastoma 1GIST 1Core Binding Factor Acute Myeloid Leukemia 1Colorectal Neoplasms 1Central Nervous System Neoplasms 1

Interventions

fludarabine phosphate 6Whole-Body Irradiation 5Therapeutics 5Mycophenolic Acid 5Cyclosporine 5Psychiatric Rehabilitation 4Peripheral Blood Stem Cell Transplantation 4midostaurin 3avapritinib 2Sunitinib 2Pentetic Acid 2Methotrexate 2Early Intervention, Educational 2Darbepoetin alfa 2Busulfan 2thymoglobulin 1ripretinib 1liposomal doxorubicin 1ibrutinib 1hydrocortisone valerate 1fludarabine 1ferrous sulfate 1ferric gluconate 1ethanolamine oleate 1denileukin diftitox 1Valganciclovir 1Trimethoprim, Sulfamethoxazole Drug Combination 1Trimethoprim 1Thiotepa 1Tacrolimus 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

2 trials
RecentStart dateEnrollment
Leukemia, Mast-Cell × avapritinib × Clear all
NCT03580655 2026-04-24

(PATHFINDER) Study to Evaluate Efficacy and Safety of Avapritinib (BLU-285), A Selective KIT Mutation-targeted Tyrosine Kinase Inhibitor, in Patients With Advanced Systemic Mastocytosis

Blueprint Medicines Corporation

Phase 2 Completed
107 enrolled 30 charts 1 FDA
LymphoidMyeloidOther hematologic neoplasm

Leukemia, Mast-Cell, Mastocytosis, Systemic

NCT02561988 2023-03-17

(EXPLORER) Study of BLU-285 in Patients With Advanced Systemic Mastocytosis (AdvSM) and Relapsed or Refractory Myeloid Malignancies

Blueprint Medicines Corporation

Phase 1 Completed
86 enrolled 1 FDA
LymphoidMyeloidOther hematologic neoplasm

Leukemia, Mast-Cell, Recurrence, Mastocytosis, Systemic

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