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Phase

Phase 2 1Phase 1/2 1

Status

Recruiting 1Active not recruiting 1

Sponsor Class

OTHER 1NIH 1

Study Type

Interventional 2

Sponsor

Cancer Type

Other hematologic neoplasm 2CNS 2

Conditions

Melanoma 23Multiple Myeloma 9Colorectal Neoplasms 9Carcinoma, Non-Small-Cell Lung 9Thyroid Neoplasms 8Glioma 8Neoplasm Metastasis 7Hematologic Neoplasms 6Thyroid Carcinoma, Anaplastic 5Pancreatic Neoplasms 5Lymphoma 5Thyroid Cancer, Papillary 4Neurofibromatosis 1 4Neoplasms 4Lung Neoplasms 3Brain Neoplasms 3Astrocytoma 3Adenocarcinoma, Follicular 3Skin Neoplasms 2Recurrence 2Rectal Neoplasms 2Prostatic Neoplasms 2Ovarian Neoplasms 2Neurofibroma, Plexiform 2Leukemia, Myelomonocytic, Juvenile 2Histiocytosis, Langerhans-Cell 2Glioblastoma 2Colonic Neoplasms 2Advanced Solid Tumors 2Uveal Melanoma 1

Interventions

fludarabine 7Cyclophosphamide 6fludarabine phosphate 5Melphalan 4thymoglobulin 3Tacrolimus 3Methotrexate 3Cytarabine 3Busulfan 3trametinib 2blinatumomab 2Whole-Body Irradiation 2Transplantation 2Thiotepa 2Specimen Handling 2Sirolimus 2Rituximab 2Peripheral Blood Stem Cell Transplantation 2Mycophenolic Acid 2Mesna 2Granulocyte Colony-Stimulating Factor 2Filgrastim 2Biopsy 2Azacitidine 2omipalisib 1merphos 1imetelstat 1hydrocortisone hemisuccinate 1Vorinostat 1Stem Cell Transplantation 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

2 trials
RecentStart dateEnrollment
Leukemia, Myelomonocytic, Juvenile × trametinib × 1 year × Clear all
NCT03190915 2026-05-27

Trametinib in Treating Patients With Relapsed or Refractory Juvenile Myelomonocytic Leukemia

National Cancer Institute (NCI)

Phase 2 Active not recruiting
10 enrolled 11 charts
CNSOther hematologic neoplasm

Neurofibromatosis 1, Leukemia, Myelomonocytic, Juvenile

NCT05849662 2026-04-15

A Phase I/II Study of Trametinib and Azacitidine for Patients With Newly Diagnosed Juvenile Myelomonocytic Leukemia

Therapeutic Advances in Childhood Leukemia Consortium

Phase 1/2 Recruiting
58 enrolled
CNSOther hematologic neoplasm

Neurofibromatosis 1, Leukemia, Myelomonocytic, Juvenile

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