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Phase

Phase 2 1Phase 1/2 1

Status

Recruiting 1Active not recruiting 1

Sponsor Class

OTHER 1NIH 1

Study Type

Interventional 2

Sponsor

Cancer Type

Other hematologic neoplasm 2CNS 2

Conditions

Melanoma 10Multiple Myeloma 7Glioma 6Neoplasm Metastasis 5Lymphoma 5Hematologic Neoplasms 5Carcinoma, Non-Small-Cell Lung 5Neurofibromatosis 1 4Pancreatic Neoplasms 3Neoplasms 3Colorectal Neoplasms 3Thyroid Neoplasms 2Neurofibroma, Plexiform 2Lung Neoplasms 2Leukemia, Myelomonocytic, Juvenile 2Glioblastoma 2Brain Neoplasms 2Astrocytoma 2Uveal Melanoma 1Uterine Neoplasms 1Uterine Cervical Neoplasms 1Urinary Bladder Neoplasms 1Thyroid Carcinoma, Anaplastic 1Thyroid Cancer, Papillary 1Stomach Neoplasms 1Sarcoma 1Refractory Differentiated Thyroid Gland Carcinoma 1Rectal Neoplasms 1Prostatic Neoplasms 1Ovarian Neoplasms 1

Interventions

fludarabine 6Cyclophosphamide 5fludarabine phosphate 4Melphalan 3Busulfan 3trametinib 2thymoglobulin 2Whole-Body Irradiation 2Tacrolimus 2Specimen Handling 2Peripheral Blood Stem Cell Transplantation 2Mycophenolic Acid 2Methotrexate 2Cytarabine 2Biopsy 2omipalisib 1merphos 1imetelstat 1hydrocortisone hemisuccinate 1blinatumomab 1Transplantation 1Thiotepa 1Spinal Puncture 1Sirolimus 1Rituximab 1Radiotherapy 1Mesna 1Levetiracetam 1Leucovorin 1Injections 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

2 trials
RecentStart dateEnrollment
Leukemia, Myelomonocytic, Juvenile × trametinib × 90 days × Clear all
NCT03190915 2026-05-27

Trametinib in Treating Patients With Relapsed or Refractory Juvenile Myelomonocytic Leukemia

National Cancer Institute (NCI)

Phase 2 Active not recruiting
10 enrolled 11 charts
CNSOther hematologic neoplasm

Neurofibromatosis 1, Leukemia, Myelomonocytic, Juvenile

NCT05849662 2026-04-15

A Phase I/II Study of Trametinib and Azacitidine for Patients With Newly Diagnosed Juvenile Myelomonocytic Leukemia

Therapeutic Advances in Childhood Leukemia Consortium

Phase 1/2 Recruiting
58 enrolled
CNSOther hematologic neoplasm

Neurofibromatosis 1, Leukemia, Myelomonocytic, Juvenile

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