Announcements Trials
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Phase

Phase 2 1

Status

Recruiting 1

Sponsor Class

OTHER 1

Study Type

Interventional 1

Sponsor

Conditions

Neurofibromatoses 3Neurofibromatosis 1 2Neurofibroma, Plexiform 2Glioma 2Vascular Malformations 1Solid Tumor, Adult 1Skin Diseases, Vascular 1Primary Malignant Peripheral Nerve Sheath Tumors 1Oligodendroglioma 1Neurofibroma 1Neurocytoma 1Neoplasms, Neuroepithelial 1NF1 1Multiple Myeloma 1Melanoma 1Lymphatic Abnormalities 1Lymphangioma, Cystic 1Lymphangioma 1Liposarcoma, Myxoid 1Liposarcoma 1Leukemia, Lymphocytic, Chronic, B-Cell 1Glioblastoma 1Ganglioneuroma 1Ganglioglioma 1Colorectal Neoplasms 1Central Nervous System Neoplasms 1Astrocytoma 1Arteriovenous Malformations 1Advanced Solid Tumor 1

Interventions

Alpelisib 2mirdametinib 1Injections, Intralesional 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

1 trials
RecentStart dateEnrollment
Lymphatic Abnormalities × mirdametinib × 1 year × Clear all
NCT05983159 2026-05-05

TARGET-VM

Murdoch Childrens Research Institute

Phase 2 Recruiting
50 enrolled

Arteriovenous Malformations, Lymphangioma, Skin Diseases, Vascular, Lymphangioma, Cystic, Lymphatic Abnormalities, Vascular Malformations

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