Announcements Trials
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Phase

Phase 2 1

Status

Recruiting 1Completed 1

Sponsor Class

INDUSTRY 2

Study Type

Observational 1Interventional 1

Sponsor

Cancer Type

Myeloid 2Other hematologic neoplasm 1Lymphoid 1

Conditions

Mastocytosis, Systemic 2Systemic Mastocytosis With an Associated Hematologic Neoplasm 1Neoplasm Metastasis 1Mastocytosis 1Leukemia, Mast-Cell 1

Interventions

avapritinib 2Denosumab 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

2 trials
RecentStart dateEnrollment
Mastocytosis, Systemic × avapritinib × 90 days × Clear all
NCT03580655 2026-04-24

(PATHFINDER) Study to Evaluate Efficacy and Safety of Avapritinib (BLU-285), A Selective KIT Mutation-targeted Tyrosine Kinase Inhibitor, in Patients With Advanced Systemic Mastocytosis

Blueprint Medicines Corporation

Phase 2 Completed
107 enrolled 30 charts 1 FDA
LymphoidMyeloidOther hematologic neoplasm

Leukemia, Mast-Cell, Mastocytosis, Systemic

NCT07255638 2026-04-20

A Non-Interventional Study in Participants With Indolent Systemic Mastocytosis (ISM) in Germany

Blueprint Medicines Corporation

Recruiting
80 enrolled
Myeloid

Mastocytosis, Mastocytosis, Systemic

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