Announcements Trials
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Phase

Phase 2 1

Status

Recruiting 2Completed 2Active not recruiting 1

Sponsor Class

INDUSTRY 1

Study Type

Interventional 1

Sponsor

Cancer Type

Myeloid 1

Conditions

Mastocytosis, Systemic 1

Interventions

avapritinib 1

Date Range

30 days90 days1 yearAll

Options

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Clinical Trials

1 trials
RecentStart dateEnrollment
Active not recruiting × Mastocytosis, Systemic × avapritinib × Clear all
NCT03731260 2025-09-23

(PIONEER) Study to Evaluate Efficacy and Safety of Avapritinib (BLU-285), A Selective KIT Mutation-targeted Tyrosine Kinase Inhibitor, Versus Placebo in Patients With Indolent Systemic Mastocytosis

Blueprint Medicines Corporation

Phase 2 Active not recruiting
251 enrolled
Myeloid

Mastocytosis, Systemic

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