Announcements Trials
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Phase

Phase 2 1Phase 1/2 1

Status

Completed 2

Sponsor Class

INDUSTRY 2

Study Type

Interventional 2

Sponsor

Cancer Type

CNS 2Sarcoma 1Gastrointestinal 1

Conditions

Carcinoma, Basal Cell 4Recurrence 3Basal Cell Nevus Syndrome 3Skin Neoplasms 2Multiple Myeloma 2Medulloblastoma 2Thrombocytosis 1Thrombocythemia, Essential 1Rhabdomyosarcoma 1Prostatic Neoplasms 1Primary Myelofibrosis 1Precursor Cell Lymphoblastic Leukemia-Lymphoma 1Polycythemia Vera 1Pancreatic Diseases 1Neuroblastoma 1Myeloproliferative Disorders 1Leukemia, Myeloid, Acute 1Leukemia 1Hepatoblastoma 1Hemorrhagic Disorders 1Hematologic Neoplasms 1Hematologic Diseases 1Glioma 1Endometrial Neoplasms 1Colonic Neoplasms 1Carcinoma 1Bone Marrow Diseases 1Blood Platelet Disorders 1Blood Coagulation Disorders 1Astrocytoma 1

Interventions

Vincristine 8Magnetic Resonance Spectroscopy 8Cyclophosphamide 7Cisplatin 6X-Rays 5Specimen Handling 5Radiotherapy 5Phantoms, Imaging 5Irinotecan 5Carboplatin 5Temozolomide 4Radiation 4Platinum 4Nuclear Medicine Department, Hospital 4Lomustine 4palbociclib 3Granulocyte Colony-Stimulating Factor 3Filgrastim 3Etoposide 3Biopsy 31,2-diaminocyclohexaneplatinum II citrate 3ulixertinib 2tipifarnib 2tazemetostat 2sonidegib 2selpercatinib 2olaparib 2merphos 2larotrectinib 2ivosidenib 2

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

2 trials
RecentStart dateEnrollment
Has results × Medulloblastoma × sonidegib × Clear all
NCT01708174 2017-08-11

A Phase II Study of Oral LDE225 in Patients With Hedge-Hog (Hh)-Pathway Activated Relapsed Medulloblastoma (MB)

Novartis

Phase 2 Completed
22 enrolled 12 charts
CNS

Medulloblastoma, Recurrence

NCT01125800 2017-03-20

A Phase I Dose Finding and Safety Study of Oral LDE225 in Children and a Phase II Portion to Assess Preliminary Efficacy in Recurrent or Refractory MB

Novartis

Phase 1/2 Completed
76 enrolled 18 charts
CNSGastrointestinalSarcoma

Astrocytoma, Glioma, Medulloblastoma, Neuroblastoma, Recurrence, Rhabdomyosarcoma, Hepatoblastoma

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