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NCT07407803 2026-04-06Evaluation of TQ-B3234 Capsules in Patients With Symptomatic, Non-Surgical Type 1 Neurofibromatosis-Associated Plexiform NeurofibromasChia Tai Tianqing Pharmaceutical Group Co., Ltd.Phase 3 Recruiting177 enrolled
NCT03975829 2026-04-02Pediatric Long-Term Follow-up and Rollover StudyNovartisPhase 4 Active not recruiting163 enrolled
NCT06360406 2026-03-31Real-World Treatment Study of Koselugo (Selumetinib)AstraZenecaRecruiting200 enrolled
NCT05028166 2026-03-27Individual Patient Compassionate Use of MirdametinibSpringWorks Therapeutics, Inc.Available