Announcements Trials
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Phase

Phase 4 1Phase 2 1

Status

Recruiting 1Active not recruiting 1

Sponsor Class

NIH 1INDUSTRY 1

Study Type

Interventional 2

Sponsor

Cancer Type

CNS 2Other hematologic neoplasm 1Myeloid 1

Conditions

Melanoma 4Multiple Myeloma 3Glioma 3Neurofibromatosis 1 2Neoplasms 2Lymphoma 2Hematologic Neoplasms 2Glioblastoma 2Astrocytoma 2Uterine Neoplasms 1Uterine Cervical Neoplasms 1Urinary Bladder Neoplasms 1Thyroid Neoplasms 1Stomach Neoplasms 1Rectal Neoplasms 1Prostatic Neoplasms 1Pancreatic Neoplasms 1Ovarian Neoplasms 1Oligodendroglioma 1Neurofibroma, Plexiform 1Neurocytoma 1Neuroblastoma 1Neoplasm Metastasis 1Lymphoma, Non-Hodgkin 1Lung Neoplasms 1Leukemia, Myelomonocytic, Juvenile 1Histiocytosis, Langerhans-Cell 1Ganglioneuroma 1Ganglioglioma 1Esophageal Neoplasms 1

Interventions

AZD 6244 4trametinib 2omipalisib 1lorlatinib 1encorafenib 1dabrafenib 1binimetinib 1abemaciclib 1Sirolimus 1N-monoacetylcystine 1Lasers, Solid-State 1Lasers 1Inhalation 1Curcumin 1Cetuximab 1Biopsy 1Acetylcysteine 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

2 trials
RecentStart dateEnrollment
Neurofibromatosis 1 × trametinib × 30 days × Clear all
NCT03975829 2026-06-02

Pediatric Long-Term Follow-up and Rollover Study

Novartis

Phase 4 Recruiting
165 enrolled
CNSMyeloid

Astrocytoma, Ganglioneuroma, Glioblastoma, Glioma, Histiocytosis, Langerhans-Cell, Neuroblastoma, Neurofibromatosis 1, Oligodendroglioma, Ganglioglioma, Neurocytoma, Neurofibroma, Plexiform

NCT03190915 2026-05-27

Trametinib in Treating Patients With Relapsed or Refractory Juvenile Myelomonocytic Leukemia

National Cancer Institute (NCI)

Phase 2 Active not recruiting
10 enrolled 11 charts
CNSOther hematologic neoplasm

Neurofibromatosis 1, Leukemia, Myelomonocytic, Juvenile

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