Announcements Trials
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Phase

Phase 2 1Phase 1/2 1Phase 1 1

Status

Active not recruiting 7Not yet recruiting 6Completed 3Withdrawn 2Recruiting 1

Sponsor Class

OTHER 2INDUSTRY 1

Study Type

Interventional 3

Sponsor

Cancer Type

CNS 3Sarcoma 1

Conditions

Carcinoma, Non-Small-Cell Lung 16Melanoma 8Lung Neoplasms 8Neoplasm Metastasis 6Colorectal Neoplasms 6Solid Tumours 5Neoplasms 5Breast Neoplasms 4Uveal Melanoma 3Thyroid Neoplasms 3Pancreatic Neoplasms 3Neurofibromatosis 1 3Colonic Neoplasms 3Thyroid Cancer, Papillary 2Carcinoma, Hepatocellular 2Biliary Tract Neoplasms 2Adult Solid Neoplasm 2Thyroid Diseases 1Thymoma 1Solid Tumors 1Small Cell Lung Carcinoma 1Sarcoma 1Renal Insufficiency 1Rectal Neoplasms 1Optic Nerve Glioma 1Non-small Cell Lung Cancer Metastatic 1Neurofibrosarcoma 1Neurofibroma, Plexiform 1Neuroblastoma 1Myelodysplastic-Myeloproliferative Diseases 1

Interventions

Lovastatin 3Deoxycholic Acid 3AZD 6244 3pirfenidone 2Vinblastine 2Transcranial Direct Current Stimulation 2Sirolimus 2Polidocanol 2Lasers, Solid-State 2Inhalation 2Acetylcysteine 2tipifarnib 1pomalidomide 1peginterferon alfa-2b 1mirdametinib 1diphenylcyclopropenone 1binimetinib 1X-Rays 1Vincristine 1Temozolomide 1Surveys and Questionnaires 1Sunitinib 1Specimen Handling 1Sorafenib 1Saline Solution 1Ranibizumab 1Radiotherapy 1Photons 1Pharmacokinetics 1Neuropsychological Tests 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

3 trials
RecentStart dateEnrollment
Completed × Neurofibromatosis 1 × AZD 6244 × Clear all
NCT03433183 2026-05-27

SARC031: MEK Inhibitor Selumetinib (AZD6244) in Combination With the mTOR Inhibitor Sirolimus for Patients With Malignant Peripheral Nerve Sheath Tumors

Sarcoma Alliance for Research through Collaboration

Phase 2 Completed
21 enrolled 12 charts
CNSSarcoma

Neurofibromatosis 1, Neurofibrosarcoma

NCT03326388 2024-04-04

INSPECT

Great Ormond Street Hospital for Children NHS Foundation Trust

Phase 1/2 Completed
14 enrolled
CNS

Neurofibromatosis 1, Neurofibroma, Plexiform, Optic Nerve Glioma

NCT04495127 2023-04-26

Selumetinib Paediatric NF1 Japan Study

AstraZeneca

Phase 1 Completed
12 enrolled
CNS

Neurofibromatosis 1

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