Announcements Trials
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Phase

Phase 2 3Phase NA 1Phase 1 1

Status

Terminated 1Completed 1Active not recruiting 1

Sponsor Class

OTHER 3

Study Type

Interventional 3

Sponsor

Cancer Type

CNS 3

Conditions

Neurofibromatosis 1 3Breast Neoplasms 3Melanoma 2Squamous Cell Carcinoma of Head and Neck 1Radiation Injuries 1Prostatic Neoplasms 1Precancerous Conditions 1Ovarian Neoplasms 1Oropharyngeal Neoplasms 1Noonan Syndrome 1Nasopharyngeal Carcinoma 1Mouth Neoplasms 1Learning Disabilities 1Laryngeal Neoplasms 1Hypopharyngeal Neoplasms 1Dyslexia 1Cognition Disorders 1Carcinoma, Ovarian Epithelial 1Carcinoma 1Breast Carcinoma In Situ 1

Interventions

AZD 6244 9trametinib 3mirdametinib 3Lovastatin 3Sirolimus 2Inhalation 2Everolimus 2Acetylcysteine 2tipifarnib 1thymoglobulin 1pirfenidone 1peginterferon alfa-2b 1omipalisib 1fludarabine 1cediranib 1binimetinib 1Vitamin D 1Vincristine 1Vinblastine 1Temozolomide 1Sunitinib 1Saline Solution 1Rituximab 1Radiotherapy 1Radiation 1Photochemotherapy 1N-monoacetylcystine 1Methotrexate 1Melphalan 1Levetiracetam 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

3 trials
RecentStart dateEnrollment
Phase 2 × Neurofibromatosis 1 × Lovastatin × Clear all
NCT02964884 2025-06-24

Interventions for Reading Disabilities in NF1

Vanderbilt University

Phase 2 Active not recruiting
120 enrolled
CNS

Dyslexia, Learning Disabilities, Neurofibromatosis 1

NCT03504501 2023-11-30

SynCoRAS

Technical University of Munich

Phase 2 Terminated
16 enrolled
CNS

Cognition Disorders, Neurofibromatosis 1, Noonan Syndrome

NCT00853580 2018-03-12

STARS

University of Alabama at Birmingham

Phase 2 Completed
146 enrolled 29 charts
CNS

Neurofibromatosis 1

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