Announcements Trials
Browse Landscape

Phase

Phase 2 1

Status

Completed 1

Sponsor Class

OTHER 1

Study Type

Interventional 1

Sponsor

Cancer Type

Classical hematology 1

Conditions

Leukemia, Myeloid, Acute 7Precursor Cell Lymphoblastic Leukemia-Lymphoma 6Myelodysplastic Syndromes 6Hematologic Neoplasms 5Lymphoma, Non-Hodgkin 4Myeloproliferative Disorders 3Leukemia, Myelogenous, Chronic, BCR-ABL Positive 3Hodgkin Disease 3Bone Marrow Failure Disorders 3Multiple Myeloma 2Lymphoma, Mantle-Cell 2Lymphoma, Follicular 2Leukemia, Lymphocytic, Chronic, B-Cell 2Leukemia, Biphenotypic, Acute 2Anemia, Refractory, with Excess of Blasts 2Vasculitis, Central Nervous System 1Stiff-Person Syndrome 1Shwachman-Diamond Syndrome 1Sarcoma, Myeloid 1Rhabdomyosarcoma 1Recurrence 1Rasmussen subacute encephalitis 1Primary Myelofibrosis 1Polyradiculoneuropathy, Chronic Inflammatory Demyelinating 1Opsoclonus-Myoclonus Syndrome 1Non-Malignant Neoplasm 1Neuromyelitis Optica 1Neurofibrosarcoma 1Neuroectodermal Tumors, Primitive, Peripheral 1Neuroblastoma 1

Interventions

fludarabine phosphate 2Peripheral Blood Stem Cell Transplantation 2treosulfan 1thymoglobulin 1X-Rays 1Whole-Body Irradiation 1Tacrolimus 1Methotrexate 1Cyclophosphamide 1Bone Marrow Transplantation 1Antilymphocyte Serum 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

1 trials
RecentStart dateEnrollment
Shwachman-Diamond Syndrome × Antilymphocyte Serum × 1 year × Clear all
NCT04965597 2026-03-09

Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)

Fred Hutchinson Cancer Center

Phase 2 Completed
40 enrolled
Classical hematology

Congenital amegakaryocytic thrombocytopenia, Bone Marrow Failure Disorders, Shwachman-Diamond Syndrome, Anemia, Hypochromic, Hemoglobinuria, Paroxysmal, Anemia, Diamond-Blackfan

Data powered by HemOnc (CC BY 4.0) Colophon âš¡