Announcements Trials
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Phase

Phase 2 1

Status

Completed 1

Sponsor Class

OTHER 1

Study Type

Interventional 1

Sponsor

Cancer Type

Classical hematology 1

Conditions

Leukemia, Myeloid, Acute 18Precursor Cell Lymphoblastic Leukemia-Lymphoma 15Myelodysplastic Syndromes 13Hematologic Neoplasms 7Myeloproliferative Disorders 6Lymphoma 6Leukemia, Myelomonocytic, Chronic 5Leukemia, Myelogenous, Chronic, BCR-ABL Positive 5Leukemia 5Graft vs Host Disease 5Primary Myelofibrosis 4Lymphoma, Non-Hodgkin 4Leukemia, Biphenotypic, Acute 4Hodgkin Disease 4Burkitt Lymphoma 4Leukemia, Lymphoid 3Leukemia, Lymphocytic, Chronic, B-Cell 3Anemia, Refractory, with Excess of Blasts 3Waldenstrom Macroglobulinemia 2Thrombocythemia, Essential 2Sezary Syndrome 2Recurrence 2Precursor T-Cell Lymphoblastic Leukemia-Lymphoma 2Precancerous Conditions 2Polycythemia Vera 2Pdgfra-Associated Chronic Eosinophilic Leukemia 2Mycosis Fungoides 2Multiple Myeloma 2Lymphoma, T-Cell, Cutaneous 2Lymphoma, Follicular 2

Interventions

treosulfan 1thymoglobulin 1fludarabine phosphate 1X-Rays 1Tacrolimus 1Peripheral Blood Stem Cell Transplantation 1Methotrexate 1Bone Marrow Transplantation 1Antilymphocyte Serum 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

1 trials
RecentStart dateEnrollment
Shwachman-Diamond Syndrome × Tacrolimus × 90 days × Clear all
NCT04965597 2026-03-09

Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)

Fred Hutchinson Cancer Center

Phase 2 Completed
40 enrolled
Classical hematology

Congenital amegakaryocytic thrombocytopenia, Bone Marrow Failure Disorders, Shwachman-Diamond Syndrome, Anemia, Hypochromic, Hemoglobinuria, Paroxysmal, Anemia, Diamond-Blackfan

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