Announcements Trials
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Phase

Phase 2 1

Status

Completed 1

Sponsor Class

OTHER 1

Study Type

Interventional 1

Sponsor

Cancer Type

Classical hematology 1

Conditions

Precursor Cell Lymphoblastic Leukemia-Lymphoma 3Leukemia, Myeloid, Acute 3beta-Thalassemia 2Myelodysplastic Syndromes 2Lymphoma, Non-Hodgkin 2Leukemia, Myelomonocytic, Juvenile 2Leukemia, Myelogenous, Chronic, BCR-ABL Positive 2Hodgkin Disease 2Hematologic Neoplasms 2Thalassemia 1Shwachman-Diamond Syndrome 1Primary Myelofibrosis 1Neurofibromatosis 1 1Neoplasm, Residual 1Multiple Myeloma 1Leukemia, Myelomonocytic, Chronic 1Leukemia, Large Granular Lymphocytic 1Leukemia 1Influenza, Human 1Hemoglobinuria, Paroxysmal 1Congenital amegakaryocytic thrombocytopenia 1Chromosome Aberrations 1Chromosome 7, monosomy 1Bone Marrow Failure Disorders 1Anemia, Sickle Cell 1Anemia, Refractory, with Excess of Blasts 1Anemia, Hypochromic 1Anemia, Diamond-Blackfan 1

Interventions

treosulfan 1thymoglobulin 1fludarabine phosphate 1X-Rays 1Tacrolimus 1Peripheral Blood Stem Cell Transplantation 1Methotrexate 1Bone Marrow Transplantation 1Antilymphocyte Serum 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

1 trials
RecentStart dateEnrollment
Shwachman-Diamond Syndrome × thymoglobulin × 90 days × Clear all
NCT04965597 2026-03-09

Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)

Fred Hutchinson Cancer Center

Phase 2 Completed
40 enrolled
Classical hematology

Congenital amegakaryocytic thrombocytopenia, Bone Marrow Failure Disorders, Shwachman-Diamond Syndrome, Anemia, Hypochromic, Hemoglobinuria, Paroxysmal, Anemia, Diamond-Blackfan

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