Announcements Trials
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Phase

Phase 2 1

Status

Completed 1

Sponsor Class

OTHER 1

Study Type

Interventional 1

Sponsor

Cancer Type

Classical hematology 1

Conditions

Leukemia 12Myelodysplastic Syndromes 11Leukemia, Myeloid, Acute 10Multiple Myeloma 8Lymphoma 7Precursor Cell Lymphoblastic Leukemia-Lymphoma 6Lymphoma, Non-Hodgkin 6Leukemia, Myelogenous, Chronic, BCR-ABL Positive 5Leukemia, Lymphocytic, Chronic, B-Cell 4Lymphoma, Follicular 3Hodgkin Disease 3Graft vs Host Disease 3Waldenstrom Macroglobulinemia 2Neoplasms, Plasma Cell 2Lymphoma, Large B-Cell, Diffuse 2Lymphoma, B-Cell, Marginal Zone 2Hematologic Neoplasms 2Wilms Tumor 1Testicular Neoplasms 1Shwachman-Diamond Syndrome 1Sarcoma, Ewing 1Sarcoma 1Rhabdomyosarcoma 1Recurrence 1Philadelphia Chromosome 1Pathologic Complete Response 1Optic Nerve Glioma 1Neuroectodermal Tumors, Primitive, Peripheral 1Neuroblastoma 1Medulloblastoma 1

Interventions

fludarabine phosphate 2Tacrolimus 2Peripheral Blood Stem Cell Transplantation 2Methotrexate 2treosulfan 1thymoglobulin 1merphos 1X-Rays 1Whole-Body Irradiation 1Mycophenolic Acid 1Melphalan 1Bone Marrow Transplantation 1Antilymphocyte Serum 1

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

1 trials
RecentStart dateEnrollment
Completed × Shwachman-Diamond Syndrome × Bone Marrow Transplantation × Clear all
NCT04965597 2026-03-09

Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)

Fred Hutchinson Cancer Center

Phase 2 Completed
40 enrolled
Classical hematology

Congenital amegakaryocytic thrombocytopenia, Bone Marrow Failure Disorders, Shwachman-Diamond Syndrome, Anemia, Hypochromic, Hemoglobinuria, Paroxysmal, Anemia, Diamond-Blackfan

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