Announcements Trials
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Phase

Phase 3 4Phase 2 1

Status

Completed 4Terminated 1Approved for marketing 1

Sponsor Class

OTHER 6INDUSTRY 6FED 1

Study Type

Interventional 5Expanded_access 1

Sponsor

Conditions

Lambert-Eaton Myasthenic Syndrome 4Myasthenia Gravis 2Nystagmus, Pathologic 1Myasthenic Syndromes, Congenital 1

Interventions

pembrolizumab 1033Carboplatin 971Paclitaxel 942Gemcitabine 799Cisplatin 757Docetaxel 698Bevacizumab 637Nivolumab 520Pemetrexed 507Capecitabine 475Cyclophosphamide 473Fluorouracil 425Dexamethasone 410Rituximab 391Oxaliplatin 352Injections 347Trastuzumab 314atezolizumab 312Cetuximab 291Leucovorin 290Irinotecan 271130-nm albumin-bound paclitaxel 257Prednisone 251Ipilimumab 244Doxorubicin 241Lenalidomide 231Fulvestrant 226fludarabine 219durvalumab 211Erlotinib Hydrochloride 196

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

6 trials
RecentStart dateEnrollment
INDUSTRY × Amifampridine × Clear all
NCT02189720 2025-03-26

EAP-001

Catalyst Pharmaceuticals, Inc.

Approved for marketing

Nystagmus, Pathologic, Lambert-Eaton Myasthenic Syndrome, Myasthenic Syndromes, Congenital

NCT03579966 2024-05-07

Long Term Safety Study of Amifampridine Phosphate in MuSK-MG (Muscle Specific Tyrosine Kinase Myasthenia Gravis)

Catalyst Pharmaceuticals, Inc.

Phase 3 Terminated
63 enrolled 10 charts

Myasthenia Gravis

NCT03304054 2024-03-12

Study to Evaluate Amifampridine Phosphate in Patients With MuSK-MG

Catalyst Pharmaceuticals, Inc.

Phase 3 Completed
93 enrolled 11 charts

Myasthenia Gravis

NCT02970162 2018-12-24

Phase 3 Study to Evaluate Efficacy of Amifampridine Phosphate in Lambert-Eaton Myasthenic Syndrome (LEMS)

Catalyst Pharmaceuticals, Inc.

Phase 3 Completed
26 enrolled 10 charts

Lambert-Eaton Myasthenic Syndrome

NCT01377922 2018-01-04

A Phase 3 Study of Amifampridine Phosphate in Patients With Lambert Eaton Myasthenic Syndrome (LEMS)

Catalyst Pharmaceuticals, Inc.

Phase 3 Completed
38 enrolled 12 charts

Lambert-Eaton Myasthenic Syndrome

NCT01511978 2017-07-11

DAPPER

Jacobus Pharmaceutical

Phase 2 Completed
32 enrolled 16 charts

Lambert-Eaton Myasthenic Syndrome

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