Clinical Trials

Anemia, Sickle Cell, Thalassemia, beta-Thalassemia

Myelodysplastic Syndromes, Myeloproliferative Disorders, beta-Thalassemia

Chromosome 7, monosomy, Anemia, Refractory, with Excess of Blasts, Chromosome Aberrations, Influenza, Human, Neurofibromatosis 1, Leukemia, Myeloid, Acute, beta-Thalassemia, Neoplasm, Residual, Hematologic Neoplasms, Precursor Cell Lymphoblastic Leukemia-Lymphoma, Leukemia, Myelomonocytic, Juvenile

Neutropenia, Severe Congenital, Autosomal Recessive 3, Anemia, Aplastic, Anemia, Sickle Cell, Hodgkin Disease, Lymphoma, Non-Hodgkin, beta-Thalassemia, Anemia, Diamond-Blackfan

Severe combined immunodeficiency due to adenosine deaminase deficiency, 3-methylcrotonyl CoA carboxylase 1 deficiency, 3-methylcrotonyl CoA carboxylase 2 deficiency, 3-Hydroxyacyl-CoA Dehydrogenase Deficiency, Ataxia with vitamin E deficiency, Beta ketothiolase deficiency, Bile acid synthesis defect, congenital, 2, Carnitine palmitoyl transferase 1A deficiency, Carnitine palmitoyl transferase 2 deficiency, Creatine deficiency, X-linked, Adrenocorticotropic hormone deficiency, Maple syrup urine disease, type 1A, Maple syrup urine disease, type 1B, Maple syrup urine disease, type 2, Congenital disorder of glycosylation type 1B, Medium chain acyl CoA dehydrogenase deficiency, N-acetyl glutamate synthetase deficiency, Niemann-Pick disease, type C2, Pyridoxine-dependent epilepsy, VLCAD deficiency, Primary hyperoxaluria type 1, Primary hyperoxaluria type 2, Waardenburg syndrome type 2, Waardenburg syndrome type 2A, Usher syndrome, type 1B, Usher syndrome, type 1C, Usher syndrome, type 1F, Amaurosis congenita of Leber, type 2, Glut1 Deficiency Syndrome, Glutaric Acidemia I, Glutathione synthetase deficiency, Brown-Vialetto-Van Laere syndrome, Methylenetetrahydrofolate reductase deficiency, Methylmalonic acidemia with homocystinuria, Methylmalonic aciduria cblA type, Methylmalonic aciduria cblB type, Pitt-Hopkins syndrome, Stickler syndrome, type 1, Stickler syndrome, type 2, Segawa syndrome, autosomal recessive, Guanidinoacetate methyltransferase deficiency, Basal ganglia disease, biotin-responsive, Acidemia, isovaleric, Acrodermatitis enteropathica, Adenine phosphoribosyltransferase deficiency, Adrenal hyperplasia, congenital, type 5, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, Hyperinsulinemic hypoglycemia, familial, 6, HHH syndrome, Glycogen Storage Disease IB, Hyperphenylalaninemia, BH4-Deficient, B, Thyroid Dyshormonogenesis 3, Thyroid Dyshormonogenesis 5, Glycogen Storage Disease IC, Carnitine-Acylcarnitine Translocase Deficiency, Glycogen Storage Disease IXB, Thyroid Dyshormonogenesis 2A, Intrinsic Factor Deficiency, Hyperparathyroidism, Neonatal Severe Primary, Diabetes Mellitus, Permanent Neonatal, With Neurologic Features, Diabetes Mellitus, Permanent Neonatal, Maturity-Onset Diabetes of the Young, Type 4, Thyroid Dyshormonogenesis 6, Thyroid Dyshormonogenesis 1, Tuberous Sclerosis 1, Molybdenum Cofactor Deficiency, Complementation Group A, Methylmalonic Aciduria due to Methylmalonyl-CoA Mutase Deficiency, Homocystinuria-Megaloblastic Anemia due to Defect in Cobalamin Metabolism, CblE Complementation Type, Tuberous Sclerosis 2, Pyridoxamine 5-Prime-Phosphate Oxidase Deficiency, Trifunctional Protein Deficiency With Myopathy And Neuropathy, Arginine-Glycine Amidinotransferase Deficiency, Jervell And Lange-Nielsen Syndrome 2, Glycogen Storage Disease, Type IXA2, Pituitary Hormone Deficiency, Combined, 1, Glycogen Storage Disease IXC, Anemia, Sickle Cell, Hemophilia B, Congenital Hypothyroidism, Cystic Fibrosis, Cystinosis, Diabetes Mellitus, Disease, Epilepsy, Epilepsies, Myoclonic, Factor VII Deficiency, Factor X Deficiency, Fragile X Syndrome, Fructose Intolerance, Galactosemias, Glycogen Storage Disease Type I, Glucosephosphate Dehydrogenase Deficiency, Glycogen Storage Disease Type II, Granulomatous Disease, Chronic, Hemophilia A, Hepatolenticular Degeneration, Homocystinuria, Hypophosphatasia, Menkes Kinky Hair Syndrome, Leukodystrophy, Globoid Cell, Leukodystrophy, Metachromatic, Mucopolysaccharidosis I, Mucopolysaccharidosis III, Mucopolysaccharidosis IV, Mucopolysaccharidosis VI, Muscular Atrophy, Spinal, Nephritis, Hereditary, Phenylketonurias, Prader-Willi Syndrome, Pseudohypoaldosteronism, Retinoblastoma, Stress Disorders, Post-Traumatic, Waardenburg Syndrome, Wolman Disease, Fructose-1,6-Diphosphatase Deficiency, Rett Syndrome, Gyrate Atrophy, Mucopolysaccharidosis II, Mucopolysaccharidosis VII, beta-Thalassemia, Angelman Syndrome, Canavan Disease, Multiple Endocrine Neoplasia Type 2b, Peroxisomal Disorders, Smith-Lemli-Opitz Syndrome, Xanthomatosis, Cerebrotendinous, Citrullinemia, Hyperargininemia, Ornithine Carbamoyltransferase Deficiency Disease, Carbamoyl-Phosphate Synthase I Deficiency Disease, Tyrosinemias, Muscular Dystrophy, Duchenne, Aortic Stenosis, Supravalvular, Hermanski-Pudlak Syndrome, Biotinidase Deficiency, Holocarboxylase Synthetase Deficiency, Jervell-Lange Nielsen Syndrome, Mineralocorticoid Excess Syndrome, Apparent, Congenital Hyperinsulinism, Niemann-Pick Disease, Type A, Niemann-Pick Disease, Type C, Familial Hypophosphatemic Rickets, X-Linked Combined Immunodeficiency Diseases, Propionic Acidemia, von Willebrand Disease, Type 3, Argininosuccinic Aciduria, Barth Syndrome, Liddle Syndrome

Alzheimer Disease, Amyloidosis, Amyotrophic Lateral Sclerosis, Anemia, Sickle Cell, Cystic Fibrosis, Ehlers-Danlos Syndrome, Gaucher Disease, Glycogen Storage Disease Type II, Huntington Disease, Myasthenia Gravis, Gangliosidosis, GM1, alpha-Thalassemia, beta-Thalassemia, Muscular Dystrophy, Duchenne, Insomnia, Fatal Familial, Rare Diseases

Glioma, beta-Thalassemia, Intracranial Hemorrhages

red meat allergy, Alopecia Areata, Alzheimer Disease, Amyloidosis, Anemia, Sickle Cell, Arthritis, Asthma, Autistic Disorder, Behcet Syndrome, Celiac Disease, Colitis, Ulcerative, Crohn Disease, Cystic Fibrosis, Dermatitis, Atopic, Diabetes Mellitus, Epilepsies, Myoclonic, Fibrosis, Fibromyalgia, Graves Disease, Heart Diseases, Hepatitis, Hypersensitivity, Kidney Diseases, Leukemia, Lupus Erythematosus, Systemic, Lymphoma, Macular Degeneration, Multiple Sclerosis, Myasthenia Gravis, Neoplasms, Parkinson Disease, Pemphigus, Psoriasis, Schizophrenia, Spondylitis, Ankylosing, Thyroid Diseases, Vasculitis, Vitiligo, beta-Thalassemia, Hidradenitis Suppurativa, Hepatitis, Autoimmune, Stroke, Pulmonary Disease, Chronic Obstructive, Scleroderma, Diffuse

Generalized Anxiety Disorder, Acquired Immunodeficiency Syndrome, Alopecia Areata, Anemia, Sickle Cell, Asthma, Bipolar Disorder, Breast Neoplasms, Celiac Disease, Uterine Cervical Neoplasms, Colitis, Ulcerative, Colonic Neoplasms, Crohn Disease, Cystic Fibrosis, Depression, Diabetes Mellitus, Down Syndrome, Endometriosis, Epilepsy, Glucosephosphate Dehydrogenase Deficiency, Hepatitis B, Huntington Disease, Sleep Initiation and Maintenance Disorders, Kidney Neoplasms, Polycystic Kidney Diseases, Leukemia, Lung Neoplasms, Lupus Erythematosus, Systemic, Lupus Nephritis, Lymphoma, Melanoma, Multiple Myeloma, Multiple Sclerosis, Muscular Atrophy, Spinal, Myositis, Myotonic Dystrophy, Ovarian Neoplasms, Pancreatic Neoplasms, Parkinson Disease, Prostatic Neoplasms, Psoriasis, Purpura, Thrombotic Thrombocytopenic, Rosacea, Sickle Cell Trait, Sjogren's Syndrome, Skin Neoplasms, Spondylitis, Ankylosing, Telangiectasia, Hereditary Hemorrhagic, Colorectal Neoplasms, Arthritis, Psoriatic, Purpura, Thrombocytopenic, Idiopathic, beta-Thalassemia, Polyradiculoneuropathy, Chronic Inflammatory Demyelinating, Muscular Dystrophy, Duchenne, Muscular Dystrophy, Facioscapulohumeral, Pulmonary Disease, Chronic Obstructive, Scleroderma, Diffuse, Renal Insufficiency, Chronic

Adrenoleukodystrophy, Hodgkin Disease, Leukemia, Lymphoma, Lymphoma, Non-Hodgkin, Motor Activity, Neoplasms, Sickle Cell Trait, Leukemia, B-Cell, Leukemia, T-Cell, Leukemia, Myeloid, Acute, beta-Thalassemia

Breast Neoplasms, Heart Diseases, beta-Thalassemia, Cardiotoxicity

beta-Thalassemia

Neoplasms, beta-Thalassemia, Hepatoblastoma

Bone Marrow Failure Disorders, Anemia, Sickle Cell, Immunologic Deficiency Syndromes, Leukemia, Lymphoma, Metabolism, Inborn Errors, Histiocytosis, beta-Thalassemia

Anemia, Sickle Cell, Metabolism, Inborn Errors, Myelodysplastic Syndromes, Leukemia, Myeloid, Acute, beta-Thalassemia, Hematologic Neoplasms, X-Linked Combined Immunodeficiency Diseases, Precursor Cell Lymphoblastic Leukemia-Lymphoma