Announcements Trials
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Phase

Phase 1 4Phase 2 1Phase 1/2 1

Status

Terminated 4Completed 2

Sponsor Class

INDUSTRY 4NETWORK 2

Study Type

Interventional 6

Sponsor

Cancer Type

CNS 2Tumor-Agnostic 1Sarcoma 1Other hematologic neoplasm 1Breast 1

Conditions

Neoplasms 2Spinal Cord Neoplasms 1Sarcoma, Kaposi 1Optic Nerve Glioma 1Oligodendroglioma 1Neurofibromatosis 2 1Neurofibromatoses 1Neoplasms by Histologic Type 1Meningioma 1Medulloblastoma 1Leukemia, Myeloid, Acute 1Leukemia, Myeloid 1HIV Infections 1Familial ependymoma 1Central Nervous System Neoplasms 1Breast Neoplasms 1Astrocytoma 1AIDS-related Kaposi sarcoma 1

Interventions

Cisplatin 3193Cyclophosphamide 3187Carboplatin 2968Radiotherapy 2784Paclitaxel 2716Gemcitabine 2569pembrolizumab 2378Bevacizumab 2206Docetaxel 2196Fluorouracil 1848Capecitabine 1828Oxaliplatin 1738Dexamethasone 1604Nivolumab 1580Doxorubicin 1501Rituximab 1487Magnetic Resonance Spectroscopy 1382Etoposide 1345Irinotecan 1245Leucovorin 1222Drug Therapy 1202Cytarabine 1130Pemetrexed 1074fludarabine 1056Specimen Handling 1009Vincristine 964Cetuximab 943Prednisone 940Trastuzumab 940Lenalidomide 937

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

6 trials
RecentStart dateEnrollment
emvododstat × Clear all
NCT03761069 2022-02-02

Study of PTC299 (Emvododstat) in Relapsed/Refractory Acute Leukemias

PTC Therapeutics

Phase 1 Terminated
33 enrolled
Other hematologic neoplasm

Leukemia, Myeloid, Neoplasms, Neoplasms by Histologic Type, Leukemia, Myeloid, Acute

NCT00704821 2019-05-10

PTC299 for Treatment of Advanced Cancer

PTC Therapeutics

Phase 1 Terminated
76 enrolled
Tumor-Agnostic

Neoplasms

NCT00911248 2019-04-12

PTC299 for Treatment of Neurofibromatosis Type 2

PTC Therapeutics

Phase 2 Terminated
11 enrolled
CNS

Neurofibromatosis 2, Neurofibromatoses

NCT00686842 2018-06-06

PTC299 in Treating Patients With HIV-Related Kaposi Sarcoma

AIDS Malignancy Consortium

Phase 1/2 Terminated
17 enrolled 7 charts
Sarcoma

AIDS-related Kaposi sarcoma, Sarcoma, Kaposi, HIV Infections

NCT00508586 2016-03-03

PTC299 and Hormonal Agent for Treatment of Metastatic Breast Cancer

PTC Therapeutics

Phase 1 Completed
33 enrolled
Breast

Breast Neoplasms

NCT01158300 2015-05-04

PTC299 in Treating Young Patients With Refractory or Recurrent Primary Central Nervous System Tumors

Pediatric Brain Tumor Consortium

Phase 1 Completed
28 enrolled
CNS

Familial ependymoma, Astrocytoma, Medulloblastoma, Meningioma, Oligodendroglioma, Spinal Cord Neoplasms, Central Nervous System Neoplasms, Optic Nerve Glioma

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