Announcements Trials
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Phase

Phase 1 4Phase 2 1Phase 1/2 1

Status

Terminated 4Completed 2

Sponsor Class

INDUSTRY 4NETWORK 2

Study Type

Interventional 6

Sponsor

Cancer Type

CNS 2Tumor-Agnostic 1Sarcoma 1Other hematologic neoplasm 1Breast 1

Conditions

Neoplasms 2Spinal Cord Neoplasms 1Sarcoma, Kaposi 1Optic Nerve Glioma 1Oligodendroglioma 1Neurofibromatosis 2 1Neurofibromatoses 1Neoplasms by Histologic Type 1Meningioma 1Medulloblastoma 1Leukemia, Myeloid, Acute 1Leukemia, Myeloid 1HIV Infections 1Familial ependymoma 1Central Nervous System Neoplasms 1Breast Neoplasms 1Astrocytoma 1AIDS-related Kaposi sarcoma 1

Interventions

Cyclophosphamide 3155Cisplatin 3151Carboplatin 2929Paclitaxel 2671Radiotherapy 2643Gemcitabine 2544pembrolizumab 2324Docetaxel 2154Bevacizumab 2126Fluorouracil 1819Capecitabine 1780Oxaliplatin 1709Dexamethasone 1589Nivolumab 1516Doxorubicin 1477Rituximab 1453Etoposide 1341Magnetic Resonance Spectroscopy 1261Irinotecan 1232Leucovorin 1212Cytarabine 1123Pemetrexed 1060Drug Therapy 1060fludarabine 1044Vincristine 956Specimen Handling 928Prednisone 924Cetuximab 919Lenalidomide 916Trastuzumab 897

Date Range

30 days90 days1 yearAll

Options

Has results Has announcements

Clinical Trials

6 trials
RecentStart dateEnrollment
Interventional × emvododstat × Clear all
NCT03761069 2022-02-02

Study of PTC299 (Emvododstat) in Relapsed/Refractory Acute Leukemias

PTC Therapeutics

Phase 1 Terminated
33 enrolled
Other hematologic neoplasm

Leukemia, Myeloid, Neoplasms, Neoplasms by Histologic Type, Leukemia, Myeloid, Acute

NCT00704821 2019-05-10

PTC299 for Treatment of Advanced Cancer

PTC Therapeutics

Phase 1 Terminated
76 enrolled
Tumor-Agnostic

Neoplasms

NCT00911248 2019-04-12

PTC299 for Treatment of Neurofibromatosis Type 2

PTC Therapeutics

Phase 2 Terminated
11 enrolled
CNS

Neurofibromatosis 2, Neurofibromatoses

NCT00686842 2018-06-06

PTC299 in Treating Patients With HIV-Related Kaposi Sarcoma

AIDS Malignancy Consortium

Phase 1/2 Terminated
17 enrolled 7 charts
Sarcoma

AIDS-related Kaposi sarcoma, Sarcoma, Kaposi, HIV Infections

NCT00508586 2016-03-03

PTC299 and Hormonal Agent for Treatment of Metastatic Breast Cancer

PTC Therapeutics

Phase 1 Completed
33 enrolled
Breast

Breast Neoplasms

NCT01158300 2015-05-04

PTC299 in Treating Young Patients With Refractory or Recurrent Primary Central Nervous System Tumors

Pediatric Brain Tumor Consortium

Phase 1 Completed
28 enrolled
CNS

Familial ependymoma, Astrocytoma, Medulloblastoma, Meningioma, Oligodendroglioma, Spinal Cord Neoplasms, Central Nervous System Neoplasms, Optic Nerve Glioma

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